subject_id,indication_icd10,indication,modality,product_name,age_at_dosing,sex,weight_kg,race_ethnicity,country,site_id,baseline_severity_score,baseline_severity_scale,prior_therapy_count,nab_titer_baseline,hla_type,conditioning_regimen,dose_vg_per_kg,infusion_date,enrollment_status
S00001,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,71,M,51.2,White,CAN,SITE_015,3.03,LDH_x_ULN,2,0.0,A*26:70,Flu_Cy_lymphodepletion,5000000.0,2024-02-22T00:00:00Z,Dosed
S00002,D66,Hemophilia A,AAV,AAV-FVIII,25,F,38.2,White,AUS,SITE_010,3.49,FVIII_pct,0,7.73,A*30:94,None,30000000000000.0,2023-05-23T00:00:00Z,Dosed
S00003,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,67,M,58.6,Black or African American,ESP,SITE_011,72.64,BM_plasma_pct,3,0.0,A*18:35,Flu_Cy_lymphodepletion,10000000.0,2024-04-05T00:00:00Z,Dosed
S00004,C91.00,B-ALL,CAR_T,CART-CD19,8,F,18.1,White,ITA,SITE_036,37.19,BM_blast_pct,5,0.0,A*03:67,Flu_Cy_lymphodepletion,2000000.0,2023-08-31T00:00:00Z,Dosed
S00005,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,F,19.9,White,ESP,SITE_022,24.37,CHOP_INTEND,0,0.66,A*03:39,None,30000000000000.0,2024-05-09T00:00:00Z,Screen Failure - nAb+
S00006,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,7,M,33.2,White,GBR,SITE_009,0.11,GMFC_MLD,0,0.0,A*16:95,Busulfan_reduced,8000000.0,2023-07-05T00:00:00Z,Dosed
S00007,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,F,55.5,White,CAN,SITE_012,3.69,LDH_x_ULN,3,0.0,A*08:55,Flu_Cy_lymphodepletion,2000000.0,2024-04-26T00:00:00Z,Dosed
S00008,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,55,F,59.8,Black or African American,AUS,SITE_002,1.72,LDH_x_ULN,3,0.0,A*11:32,Flu_Cy_lymphodepletion,1000000.0,2023-03-25T00:00:00Z,Dosed
S00009,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,8,F,23.7,Asian,ITA,SITE_018,20.67,NSAA,2,3.56,A*34:26,None,60000000000000.0,2023-12-29T00:00:00Z,Dosed
S00010,D66,Hemophilia A,AAV,AAV-FVIII,29,M,41.6,White,AUS,SITE_018,4.82,FVIII_pct,1,11.47,A*32:43,None,110000000000000.0,2023-01-20T00:00:00Z,Dosed
S00011,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,12,M,17.1,White,ITA,SITE_003,5.82,Hb_g_dL,3,0.0,A*18:78,Busulfan_full,2000000.0,2023-01-28T00:00:00Z,Dosed
S00012,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,49,M,57.7,Black or African American,DEU,SITE_009,45.1,BM_plasma_pct,4,0.0,A*14:23,Flu_Cy_lymphodepletion,2000000.0,2023-03-23T00:00:00Z,Dosed
S00013,C91.00,B-ALL,CAR_T,CART-CD19,17,F,26.8,White,USA,SITE_011,46.65,BM_blast_pct,4,0.0,A*14:43,Flu_Cy_lymphodepletion,5000000.0,2024-02-26T00:00:00Z,Dosed
S00014,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,49,M,58.3,White,CAN,SITE_020,3.05,LDH_x_ULN,3,0.0,A*08:73,Flu_Cy_lymphodepletion,2000000.0,2023-05-14T00:00:00Z,Dosed
S00015,D66,Hemophilia A,AAV,AAV-FVIII,21,M,33.3,White,CAN,SITE_025,1.55,FVIII_pct,0,10.91,A*04:01,None,60000000000000.0,2023-04-12T00:00:00Z,Screen Failure - nAb+
S00016,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,29,M,17.3,White,USA,SITE_023,8.36,Hb_g_dL,5,0.0,A*29:49,Busulfan_full,2000000.0,2024-04-05T00:00:00Z,Dosed
S00017,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,62,M,55.4,Hispanic or Latino,GBR,SITE_011,42.16,BCVA_letters,1,130.09,A*16:90,None,60000000000000.0,2023-02-12T00:00:00Z,Screen Failure - nAb+
S00018,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,21.5,Black or African American,GBR,SITE_012,20.35,CHOP_INTEND,0,20.82,A*28:08,None,60000000000000.0,2023-01-17T00:00:00Z,Dosed
S00019,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,40,M,38.6,Black or African American,AUS,SITE_029,3.22,LDH_x_ULN,6,0.0,A*11:13,Flu_Cy_lymphodepletion,10000000.0,2023-03-21T00:00:00Z,Dosed
S00020,C91.00,B-ALL,CAR_T,CART-CD19,12,M,14.7,White,ITA,SITE_032,89.47,BM_blast_pct,4,0.0,A*10:01,Flu_Cy_lymphodepletion,10000000.0,2023-01-09T00:00:00Z,Dosed
S00021,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,83,F,73.2,Hispanic or Latino,USA,SITE_036,2.61,LDH_x_ULN,2,0.0,A*22:18,Flu_Cy_lymphodepletion,2000000.0,2024-01-25T00:00:00Z,Dosed
S00022,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,12,M,26.5,Hispanic or Latino,USA,SITE_008,6.38,Hb_g_dL,2,0.0,A*06:23,Treosulfan,5000000.0,2024-03-29T00:00:00Z,Dosed
S00023,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,F,19.2,Black or African American,USA,SITE_022,3.4,GMFC_MLD,2,0.0,A*10:75,Treosulfan,8000000.0,2023-03-22T00:00:00Z,Dosed
S00024,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,64,M,55.2,White,DEU,SITE_018,34.7,BM_plasma_pct,4,0.0,A*27:88,Flu_Cy_lymphodepletion,5000000.0,2023-08-02T00:00:00Z,Dosed
S00025,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,64,M,50.7,White,ESP,SITE_008,3.58,LDH_x_ULN,6,0.0,A*32:24,Flu_Cy_lymphodepletion,1000000.0,2023-07-05T00:00:00Z,Dosed
S00026,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,0,F,15.2,White,FRA,SITE_004,24.24,NSAA,2,12.86,A*33:56,None,30000000000000.0,2023-02-26T00:00:00Z,Dosed
S00027,D66,Hemophilia A,AAV,AAV-FVIII,30,F,28.8,White,USA,SITE_009,3.97,FVIII_pct,1,106.39,A*01:97,None,200000000000000.0,2024-03-10T00:00:00Z,Dosed
S00028,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,20.0,Black or African American,ESP,SITE_023,20.23,CHOP_INTEND,1,28.69,A*20:92,None,30000000000000.0,2023-09-10T00:00:00Z,Screen Failure - nAb+
S00029,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,20.7,White,GBR,SITE_007,23.58,NSAA,0,18.79,A*12:72,None,200000000000000.0,2023-04-18T00:00:00Z,Dosed
S00030,C91.00,B-ALL,CAR_T,CART-CD19,11,F,17.2,White,USA,SITE_040,58.93,BM_blast_pct,2,0.0,A*02:46,Flu_Cy_lymphodepletion,2000000.0,2023-05-21T00:00:00Z,Dosed
S00031,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,65,M,66.3,Black or African American,ESP,SITE_020,1.33,LDH_x_ULN,3,0.0,A*09:14,Flu_Cy_lymphodepletion,2000000.0,2023-06-18T00:00:00Z,Dosed
S00032,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,F,24.7,Not Reported,JPN,SITE_015,0.43,GMFC_MLD,2,0.0,A*14:14,Treosulfan,3000000.0,2023-05-01T00:00:00Z,Dosed
S00033,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,16.7,White,ITA,SITE_021,7.01,Hb_g_dL,2,0.0,A*16:16,Busulfan_full,5000000.0,2023-07-22T00:00:00Z,Dosed
S00034,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,14,M,12.5,White,ITA,SITE_005,7.09,Hb_g_dL,5,0.0,A*02:21,Busulfan_reduced,5000000.0,2023-08-09T00:00:00Z,Dosed
S00035,D66,Hemophilia A,AAV,AAV-FVIII,32,M,38.0,Hispanic or Latino,USA,SITE_025,2.65,FVIII_pct,0,16.08,A*07:25,None,60000000000000.0,2024-01-19T00:00:00Z,Dosed
S00036,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,11.5,White,ESP,SITE_010,17.43,NSAA,0,2.2,A*06:08,None,60000000000000.0,2023-01-02T00:00:00Z,Dosed
S00037,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,15.7,White,JPN,SITE_034,15.84,NSAA,1,7.45,A*07:94,None,110000000000000.0,2023-09-18T00:00:00Z,Dosed
S00038,D66,Hemophilia A,AAV,AAV-FVIII,54,M,57.5,White,USA,SITE_011,1.12,FVIII_pct,1,9.94,A*05:01,None,200000000000000.0,2024-05-09T00:00:00Z,Dosed
S00039,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,32,M,34.6,White,ITA,SITE_034,9.27,Hb_g_dL,6,0.0,A*28:73,Busulfan_reduced,3000000.0,2024-03-29T00:00:00Z,Dosed
S00040,C91.00,B-ALL,CAR_T,CART-CD19,15,M,19.8,White,USA,SITE_003,65.48,BM_blast_pct,5,0.0,A*02:74,Flu_Cy_lymphodepletion,5000000.0,2024-03-04T00:00:00Z,Dosed
S00041,D66,Hemophilia A,AAV,AAV-FVIII,54,F,44.8,Black or African American,JPN,SITE_001,4.97,FVIII_pct,0,2.61,A*10:39,None,30000000000000.0,2024-03-06T00:00:00Z,Dosed
S00042,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,F,57.4,Hispanic or Latino,USA,SITE_026,3.18,LDH_x_ULN,3,0.0,A*25:46,Flu_Cy_lymphodepletion,2000000.0,2023-12-23T00:00:00Z,Dosed
S00043,C91.00,B-ALL,CAR_T,CART-CD19,1,M,19.4,White,ITA,SITE_008,69.08,BM_blast_pct,6,0.0,A*29:58,Flu_Cy_lymphodepletion,1000000.0,2024-06-17T00:00:00Z,Dosed
S00044,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,24,F,36.6,White,DEU,SITE_031,7.21,Hb_g_dL,5,0.0,A*13:93,Treosulfan,3000000.0,2024-02-01T00:00:00Z,Dosed
S00045,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,60,F,63.1,White,JPN,SITE_030,2.26,LDH_x_ULN,6,0.0,A*07:64,Flu_Cy_lymphodepletion,2000000.0,2023-07-04T00:00:00Z,Dosed
S00046,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,57,M,54.9,White,GBR,SITE_027,2.97,LDH_x_ULN,5,0.0,A*23:30,Flu_Cy_lymphodepletion,1000000.0,2024-04-24T00:00:00Z,Dosed
S00047,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,34,F,25.6,White,GBR,SITE_037,4.52,Hb_g_dL,5,0.0,A*30:27,Treosulfan,2000000.0,2023-06-01T00:00:00Z,Dosed
S00048,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,25,F,35.8,White,GBR,SITE_022,9.81,Hb_g_dL,5,0.0,A*20:60,Treosulfan,2000000.0,2023-06-16T00:00:00Z,Dosed
S00049,C91.00,B-ALL,CAR_T,CART-CD19,20,F,30.6,Black or African American,ITA,SITE_022,51.0,BM_blast_pct,2,0.0,A*24:86,Flu_Cy_lymphodepletion,10000000.0,2023-11-26T00:00:00Z,Dosed
S00050,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,F,21.8,White,AUS,SITE_022,20.86,NSAA,1,2.54,A*22:80,None,200000000000000.0,2023-08-06T00:00:00Z,Dosed
S00051,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,F,22.0,Asian,CAN,SITE_040,24.68,NSAA,2,226.6,A*22:45,None,15000000000000.0,2023-05-10T00:00:00Z,Dosed
S00052,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,18.7,Black or African American,GBR,SITE_017,15.47,CHOP_INTEND,1,36.06,A*28:56,None,110000000000000.0,2023-07-17T00:00:00Z,Dosed
S00053,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,49,F,60.9,White,USA,SITE_028,1.35,LDH_x_ULN,5,0.0,A*04:39,Flu_Cy_lymphodepletion,2000000.0,2024-06-23T00:00:00Z,Dosed
S00054,C91.00,B-ALL,CAR_T,CART-CD19,4,M,28.4,Black or African American,AUS,SITE_038,88.75,BM_blast_pct,5,0.0,A*03:92,Flu_Cy_lymphodepletion,1000000.0,2023-11-14T00:00:00Z,Dosed
S00055,C91.00,B-ALL,CAR_T,CART-CD19,12,F,20.1,White,JPN,SITE_029,36.46,BM_blast_pct,6,0.0,A*06:42,Flu_Cy_lymphodepletion,5000000.0,2023-10-26T00:00:00Z,Dosed
S00056,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,62,F,59.8,Not Reported,USA,SITE_040,2.55,LDH_x_ULN,2,0.0,A*04:67,Flu_Cy_lymphodepletion,5000000.0,2023-03-05T00:00:00Z,Dosed
S00057,D66,Hemophilia A,AAV,AAV-FVIII,49,M,54.2,White,CAN,SITE_015,2.41,FVIII_pct,2,19.71,A*24:82,None,60000000000000.0,2024-03-19T00:00:00Z,Dosed
S00058,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,53,M,64.0,Asian,USA,SITE_020,41.26,BCVA_letters,0,8.25,A*05:90,None,110000000000000.0,2023-06-25T00:00:00Z,Screen Failure - nAb+
S00059,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,21.4,White,USA,SITE_004,24.84,NSAA,1,5.71,A*12:64,None,15000000000000.0,2024-03-20T00:00:00Z,Dosed
S00060,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,4.0,Asian,ITA,SITE_022,30.48,CHOP_INTEND,0,5.87,A*04:54,None,15000000000000.0,2023-11-14T00:00:00Z,Screen Failure - nAb+
S00061,C91.00,B-ALL,CAR_T,CART-CD19,12,M,23.4,White,USA,SITE_013,39.25,BM_blast_pct,3,0.0,A*22:21,Flu_Cy_lymphodepletion,5000000.0,2024-02-10T00:00:00Z,Dosed
S00062,D66,Hemophilia A,AAV,AAV-FVIII,43,M,42.0,White,USA,SITE_033,2.59,FVIII_pct,2,10.82,A*34:97,None,15000000000000.0,2023-04-07T00:00:00Z,Dosed
S00063,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,31,F,48.5,Hispanic or Latino,DEU,SITE_019,17.73,BCVA_letters,0,4.44,A*33:29,None,200000000000000.0,2024-02-01T00:00:00Z,Dosed
S00064,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,50,F,69.7,Black or African American,FRA,SITE_002,1.15,LDH_x_ULN,6,0.0,A*21:37,Flu_Cy_lymphodepletion,2000000.0,2023-12-01T00:00:00Z,Dosed
S00065,C91.00,B-ALL,CAR_T,CART-CD19,4,F,5.0,Black or African American,USA,SITE_007,42.6,BM_blast_pct,3,0.0,A*05:52,Flu_Cy_lymphodepletion,1000000.0,2023-06-19T00:00:00Z,Dosed
S00066,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,45,F,51.6,White,USA,SITE_009,41.31,BCVA_letters,2,17.43,A*22:83,None,60000000000000.0,2023-02-21T00:00:00Z,Dosed
S00067,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,48,F,54.6,White,FRA,SITE_019,16.84,BCVA_letters,1,2.02,A*01:21,None,60000000000000.0,2023-02-23T00:00:00Z,Dosed
S00068,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,26.8,White,ESP,SITE_035,7.28,Hb_g_dL,3,0.0,A*13:24,Busulfan_full,3000000.0,2023-07-12T00:00:00Z,Dosed
S00069,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,F,13.9,Hispanic or Latino,USA,SITE_038,12.5,CHOP_INTEND,2,0.59,A*04:46,None,15000000000000.0,2023-08-08T00:00:00Z,Dosed
S00070,D66,Hemophilia A,AAV,AAV-FVIII,50,F,60.3,White,USA,SITE_006,1.18,FVIII_pct,2,15.39,A*03:32,None,30000000000000.0,2024-05-27T00:00:00Z,Dosed
S00071,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,F,14.1,Not Reported,GBR,SITE_020,20.91,NSAA,0,8.34,A*34:79,None,200000000000000.0,2024-03-05T00:00:00Z,Dosed
S00072,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,22,M,35.3,White,ITA,SITE_032,6.36,Hb_g_dL,6,0.0,A*20:36,Treosulfan,3000000.0,2023-08-26T00:00:00Z,Dosed
S00073,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,62,F,43.9,White,DEU,SITE_031,52.55,BM_plasma_pct,3,0.0,A*33:56,Flu_Cy_lymphodepletion,2000000.0,2023-09-07T00:00:00Z,Dosed
S00074,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,24,F,26.8,White,USA,SITE_016,6.38,Hb_g_dL,3,0.0,A*06:50,Treosulfan,5000000.0,2023-07-30T00:00:00Z,Dosed
S00075,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,F,18.1,White,FRA,SITE_034,33.19,CHOP_INTEND,0,16.96,A*21:98,None,110000000000000.0,2023-12-21T00:00:00Z,Screen Failure - nAb+
S00076,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,18,F,22.6,White,CAN,SITE_025,8.72,Hb_g_dL,2,0.0,A*32:56,Busulfan_full,2000000.0,2023-07-01T00:00:00Z,Dosed
S00077,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,29.8,White,JPN,SITE_023,7.32,Hb_g_dL,5,0.0,A*30:87,Treosulfan,3000000.0,2024-04-04T00:00:00Z,Dosed
S00078,C91.00,B-ALL,CAR_T,CART-CD19,13,M,20.9,White,ITA,SITE_009,87.75,BM_blast_pct,4,0.0,A*03:95,Flu_Cy_lymphodepletion,10000000.0,2024-04-07T00:00:00Z,Dosed
S00079,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,9,F,21.7,White,USA,SITE_005,38.38,BCVA_letters,1,5.2,A*17:63,None,60000000000000.0,2024-01-29T00:00:00Z,Dosed
S00080,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,76,M,65.4,White,ITA,SITE_036,3.51,LDH_x_ULN,5,0.0,A*03:28,Flu_Cy_lymphodepletion,5000000.0,2023-06-14T00:00:00Z,Dosed
S00081,C91.00,B-ALL,CAR_T,CART-CD19,26,M,36.2,White,DEU,SITE_028,35.62,BM_blast_pct,5,0.0,A*23:12,Flu_Cy_lymphodepletion,2000000.0,2024-03-02T00:00:00Z,Dosed
S00082,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,24,M,34.1,White,ITA,SITE_018,4.75,Hb_g_dL,2,0.0,A*17:34,Busulfan_full,2000000.0,2023-10-04T00:00:00Z,Dosed
S00083,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,65,F,75.4,White,CAN,SITE_024,3.61,LDH_x_ULN,5,0.0,A*31:63,Flu_Cy_lymphodepletion,2000000.0,2023-08-20T00:00:00Z,Dosed
S00084,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,13.6,Not Reported,FRA,SITE_039,14.57,NSAA,0,26.64,A*24:52,None,60000000000000.0,2023-07-29T00:00:00Z,Dosed
S00085,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,F,21.3,Hispanic or Latino,USA,SITE_038,23.37,CHOP_INTEND,0,3.63,A*30:56,None,15000000000000.0,2023-08-03T00:00:00Z,Dosed
S00086,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,4.0,White,JPN,SITE_008,17.15,CHOP_INTEND,0,47.47,A*33:67,None,60000000000000.0,2023-03-10T00:00:00Z,Dosed
S00087,C91.00,B-ALL,CAR_T,CART-CD19,1,F,18.9,Other,ESP,SITE_026,76.73,BM_blast_pct,2,0.0,A*11:54,Flu_Cy_lymphodepletion,2000000.0,2023-10-21T00:00:00Z,Dosed
S00088,D66,Hemophilia A,AAV,AAV-FVIII,38,F,51.4,White,FRA,SITE_019,2.55,FVIII_pct,0,8.43,A*13:12,None,110000000000000.0,2024-01-26T00:00:00Z,Screen Failure - nAb+
S00089,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,12.4,Black or African American,USA,SITE_004,16.21,NSAA,0,0.54,A*10:96,None,60000000000000.0,2023-04-29T00:00:00Z,Dosed
S00090,D67,Hemophilia B,AAV,AAV-FIX-Padua,32,F,26.1,White,ITA,SITE_002,1.61,FIX_pct,2,3.28,A*03:15,None,30000000000000.0,2023-07-16T00:00:00Z,Screen Failure - nAb+
S00091,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,F,22.6,Asian,CAN,SITE_035,26.1,NSAA,1,43.18,A*05:35,None,110000000000000.0,2023-02-18T00:00:00Z,Dosed
S00092,C91.00,B-ALL,CAR_T,CART-CD19,29,M,43.1,White,GBR,SITE_031,60.13,BM_blast_pct,4,0.0,A*07:61,Flu_Cy_lymphodepletion,2000000.0,2023-04-11T00:00:00Z,Dosed
S00093,D66,Hemophilia A,AAV,AAV-FVIII,24,M,39.2,Black or African American,ESP,SITE_037,4.75,FVIII_pct,0,2.01,A*28:11,None,30000000000000.0,2023-09-26T00:00:00Z,Screen Failure - nAb+
S00094,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,24,M,28.3,Not Reported,USA,SITE_020,5.91,Hb_g_dL,6,0.0,A*15:96,Busulfan_full,5000000.0,2023-11-17T00:00:00Z,Dosed
S00095,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,34,F,41.1,Not Reported,USA,SITE_019,9.59,Hb_g_dL,3,0.0,A*17:71,Busulfan_full,5000000.0,2024-03-19T00:00:00Z,Dosed
S00096,C91.00,B-ALL,CAR_T,CART-CD19,11,F,34.4,Black or African American,USA,SITE_035,66.02,BM_blast_pct,3,0.0,A*12:43,Flu_Cy_lymphodepletion,5000000.0,2024-02-25T00:00:00Z,Dosed
S00097,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,15,M,29.2,Asian,ESP,SITE_015,6.95,Hb_g_dL,4,0.0,A*17:46,Busulfan_reduced,2000000.0,2023-11-19T00:00:00Z,Dosed
S00098,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,17.7,Asian,JPN,SITE_009,16.81,CHOP_INTEND,2,138.99,A*04:94,None,60000000000000.0,2023-03-25T00:00:00Z,Dosed
S00099,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,7,M,24.4,Hispanic or Latino,JPN,SITE_031,27.7,CHOP_INTEND,2,25.26,A*06:78,None,30000000000000.0,2024-03-09T00:00:00Z,Dosed
S00100,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,4,M,17.6,Black or African American,USA,SITE_034,0.42,GMFC_MLD,2,0.0,A*15:48,Busulfan_full,8000000.0,2023-11-11T00:00:00Z,Dosed
S00101,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,70,M,59.5,White,JPN,SITE_014,38.82,BM_plasma_pct,3,0.0,A*08:46,Flu_Cy_lymphodepletion,2000000.0,2023-07-31T00:00:00Z,Dosed
S00102,C91.00,B-ALL,CAR_T,CART-CD19,1,F,31.7,White,DEU,SITE_006,53.52,BM_blast_pct,5,0.0,A*11:85,Flu_Cy_lymphodepletion,2000000.0,2024-05-01T00:00:00Z,Dosed
S00103,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,23,F,41.6,Black or African American,USA,SITE_001,10.0,Hb_g_dL,6,0.0,A*17:61,Busulfan_reduced,5000000.0,2024-03-25T00:00:00Z,Dosed
S00104,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,M,26.7,White,AUS,SITE_024,2.97,GMFC_MLD,1,0.0,A*17:40,Busulfan_reduced,5000000.0,2024-02-17T00:00:00Z,Dosed
S00105,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,48,M,40.9,Asian,ITA,SITE_003,3.98,LDH_x_ULN,6,0.0,A*23:86,Flu_Cy_lymphodepletion,1000000.0,2024-04-25T00:00:00Z,Dosed
S00106,C91.00,B-ALL,CAR_T,CART-CD19,18,M,26.8,Black or African American,ITA,SITE_038,47.4,BM_blast_pct,6,0.0,A*19:61,Flu_Cy_lymphodepletion,2000000.0,2023-04-27T00:00:00Z,Dosed
S00107,D66,Hemophilia A,AAV,AAV-FVIII,18,M,22.9,White,USA,SITE_003,3.73,FVIII_pct,2,2.66,A*26:18,None,200000000000000.0,2024-03-14T00:00:00Z,Dosed
S00108,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,20,F,30.1,Black or African American,CAN,SITE_033,6.94,Hb_g_dL,6,0.0,A*10:34,Treosulfan,3000000.0,2023-05-23T00:00:00Z,Dosed
S00109,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,18.7,Asian,ITA,SITE_031,19.46,CHOP_INTEND,2,1.26,A*29:67,None,110000000000000.0,2023-11-05T00:00:00Z,Dosed
S00110,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,35,M,49.0,White,ITA,SITE_030,34.45,BM_plasma_pct,6,0.0,A*05:39,Flu_Cy_lymphodepletion,2000000.0,2024-02-08T00:00:00Z,Dosed
S00111,D66,Hemophilia A,AAV,AAV-FVIII,18,M,19.7,White,DEU,SITE_020,4.45,FVIII_pct,1,2.66,A*22:14,None,60000000000000.0,2023-03-30T00:00:00Z,Dosed
S00112,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,30.4,Black or African American,DEU,SITE_004,15.37,NSAA,2,43.4,A*05:20,None,110000000000000.0,2023-04-11T00:00:00Z,Dosed
S00113,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,34,M,40.4,Hispanic or Latino,FRA,SITE_033,7.06,Hb_g_dL,5,0.0,A*10:12,Busulfan_full,2000000.0,2023-03-14T00:00:00Z,Dosed
S00114,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,58,M,78.9,Hispanic or Latino,ITA,SITE_016,32.81,mNIS_plus_7,0,0.0,A*06:78,None,0.7,2023-08-23T00:00:00Z,Dosed
S00115,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,28.3,Hispanic or Latino,JPN,SITE_003,14.71,NSAA,0,33.41,A*19:30,None,110000000000000.0,2023-12-01T00:00:00Z,Dosed
S00116,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,63,M,61.4,Other,USA,SITE_030,52.06,BM_plasma_pct,2,0.0,A*30:19,Flu_Cy_lymphodepletion,5000000.0,2024-06-15T00:00:00Z,Dosed
S00117,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,68,F,58.9,White,JPN,SITE_040,2.51,LDH_x_ULN,3,0.0,A*23:50,Flu_Cy_lymphodepletion,5000000.0,2023-11-11T00:00:00Z,Dosed
S00118,C91.00,B-ALL,CAR_T,CART-CD19,10,F,17.9,White,JPN,SITE_030,69.07,BM_blast_pct,3,0.0,A*18:79,Flu_Cy_lymphodepletion,1000000.0,2023-07-01T00:00:00Z,Dosed
S00119,D66,Hemophilia A,AAV,AAV-FVIII,18,F,28.6,Not Reported,JPN,SITE_016,3.55,FVIII_pct,1,91.62,A*03:97,None,200000000000000.0,2023-02-20T00:00:00Z,Dosed
S00120,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,65,F,62.8,Asian,ITA,SITE_016,108.4,mNIS_plus_7,1,0.0,A*31:77,None,0.3,2023-05-15T00:00:00Z,Dosed
S00121,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,51,F,53.6,Asian,JPN,SITE_038,47.61,mNIS_plus_7,0,0.0,A*32:70,None,0.3,2023-11-01T00:00:00Z,Dosed
S00122,C91.00,B-ALL,CAR_T,CART-CD19,21,M,34.8,Hispanic or Latino,JPN,SITE_002,50.77,BM_blast_pct,4,0.0,A*33:85,Flu_Cy_lymphodepletion,1000000.0,2023-07-14T00:00:00Z,Dosed
S00123,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,12.8,White,JPN,SITE_022,29.48,CHOP_INTEND,1,205.3,A*28:23,None,30000000000000.0,2023-01-15T00:00:00Z,Dosed
S00124,D66,Hemophilia A,AAV,AAV-FVIII,21,F,30.8,Asian,CAN,SITE_022,2.9,FVIII_pct,0,10.63,A*16:31,None,200000000000000.0,2023-01-10T00:00:00Z,Dosed
S00125,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,21.5,White,AUS,SITE_011,32.57,CHOP_INTEND,2,3.26,A*29:33,None,60000000000000.0,2023-04-02T00:00:00Z,Dosed
S00126,D67,Hemophilia B,AAV,AAV-FIX-Padua,18,M,16.4,White,USA,SITE_040,1.3,FIX_pct,0,1.98,A*05:73,None,30000000000000.0,2023-02-15T00:00:00Z,Dosed
S00127,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,22,F,30.2,White,JPN,SITE_038,7.79,Hb_g_dL,5,0.0,A*24:34,Busulfan_full,3000000.0,2023-02-06T00:00:00Z,Dosed
S00128,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,M,13.3,White,USA,SITE_032,18.62,NSAA,2,18.91,A*22:84,None,60000000000000.0,2023-02-11T00:00:00Z,Dosed
S00129,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,24.9,Black or African American,ESP,SITE_037,17.38,CHOP_INTEND,2,34.43,A*20:34,None,30000000000000.0,2023-06-03T00:00:00Z,Screen Failure - nAb+
S00130,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,82,F,73.0,Black or African American,ITA,SITE_025,84.61,mNIS_plus_7,2,0.0,A*21:08,None,1.0,2023-08-30T00:00:00Z,Dosed
S00131,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,23.8,White,AUS,SITE_030,17.32,NSAA,2,3.93,A*29:04,None,15000000000000.0,2024-06-02T00:00:00Z,Dosed
S00132,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,82,F,74.8,White,FRA,SITE_039,60.1,BM_plasma_pct,4,0.0,A*34:73,Flu_Cy_lymphodepletion,1000000.0,2023-02-08T00:00:00Z,Dosed
S00133,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,64,M,51.9,White,ITA,SITE_019,106.98,mNIS_plus_7,1,0.0,A*16:58,None,0.1,2023-08-19T00:00:00Z,Dosed
S00134,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,25.6,Asian,USA,SITE_022,6.13,Hb_g_dL,5,0.0,A*08:56,Treosulfan,2000000.0,2023-02-27T00:00:00Z,Dosed
S00135,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,60,F,60.5,Black or African American,CAN,SITE_013,90.77,mNIS_plus_7,1,0.0,A*06:23,None,0.1,2024-05-04T00:00:00Z,Dosed
S00136,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,24.8,Not Reported,JPN,SITE_009,17.17,CHOP_INTEND,1,9.38,A*09:63,None,30000000000000.0,2024-02-10T00:00:00Z,Screen Failure - nAb+
S00137,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,5,M,16.4,Hispanic or Latino,CAN,SITE_017,1.22,GMFC_MLD,2,0.0,A*13:52,Treosulfan,8000000.0,2023-05-02T00:00:00Z,Dosed
S00138,D67,Hemophilia B,AAV,AAV-FIX-Padua,45,F,39.5,Hispanic or Latino,GBR,SITE_024,2.08,FIX_pct,2,1.55,A*22:54,None,110000000000000.0,2023-10-30T00:00:00Z,Dosed
S00139,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,63,F,57.0,Asian,JPN,SITE_014,1.99,LDH_x_ULN,4,0.0,A*05:43,Flu_Cy_lymphodepletion,1000000.0,2023-10-15T00:00:00Z,Dosed
S00140,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,1,M,16.0,Black or African American,AUS,SITE_008,17.91,CHOP_INTEND,0,3.01,A*09:65,None,60000000000000.0,2023-05-29T00:00:00Z,Screen Failure - nAb+
S00141,D67,Hemophilia B,AAV,AAV-FIX-Padua,43,M,39.6,White,USA,SITE_034,1.62,FIX_pct,1,18.5,A*21:67,None,30000000000000.0,2023-07-26T00:00:00Z,Dosed
S00142,D67,Hemophilia B,AAV,AAV-FIX-Padua,47,F,49.2,White,USA,SITE_024,3.2,FIX_pct,2,10.28,A*31:20,None,60000000000000.0,2023-12-23T00:00:00Z,Dosed
S00143,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,54,F,44.3,White,ITA,SITE_013,53.86,BM_plasma_pct,5,0.0,A*13:73,Flu_Cy_lymphodepletion,1000000.0,2024-02-01T00:00:00Z,Dosed
S00144,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,75,F,68.3,White,USA,SITE_022,78.83,mNIS_plus_7,1,0.0,A*22:77,None,0.7,2024-03-13T00:00:00Z,Dosed
S00145,D66,Hemophilia A,AAV,AAV-FVIII,41,M,37.4,Black or African American,ESP,SITE_010,1.17,FVIII_pct,2,0.84,A*08:16,None,30000000000000.0,2023-02-14T00:00:00Z,Screen Failure - nAb+
S00146,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,32.0,Hispanic or Latino,USA,SITE_022,9.7,Hb_g_dL,2,0.0,A*18:94,Busulfan_reduced,2000000.0,2024-04-16T00:00:00Z,Dosed
S00147,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,17,F,20.7,Black or African American,JPN,SITE_032,9.4,Hb_g_dL,2,0.0,A*03:61,Treosulfan,3000000.0,2023-09-17T00:00:00Z,Dosed
S00148,D67,Hemophilia B,AAV,AAV-FIX-Padua,47,M,36.2,White,DEU,SITE_029,4.4,FIX_pct,2,35.89,A*25:50,None,30000000000000.0,2023-06-18T00:00:00Z,Screen Failure - nAb+
S00149,D66,Hemophilia A,AAV,AAV-FVIII,28,F,41.5,White,DEU,SITE_009,2.86,FVIII_pct,1,45.19,A*33:10,None,200000000000000.0,2024-05-26T00:00:00Z,Dosed
S00150,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,11.7,Black or African American,AUS,SITE_020,16.45,CHOP_INTEND,2,1.32,A*22:97,None,30000000000000.0,2023-03-23T00:00:00Z,Dosed
S00151,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,40,F,35.7,White,DEU,SITE_020,3.26,LDH_x_ULN,2,0.0,A*10:51,Flu_Cy_lymphodepletion,2000000.0,2023-01-14T00:00:00Z,Dosed
S00152,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,64,F,67.1,Other,AUS,SITE_011,35.79,BM_plasma_pct,5,0.0,A*13:87,Flu_Cy_lymphodepletion,5000000.0,2023-09-22T00:00:00Z,Dosed
S00153,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,11.2,White,FRA,SITE_012,15.96,NSAA,0,22.54,A*15:54,None,30000000000000.0,2023-05-26T00:00:00Z,Screen Failure - nAb+
S00154,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,31,F,26.0,Black or African American,GBR,SITE_031,10.48,BCVA_letters,0,67.03,A*12:45,None,200000000000000.0,2023-08-01T00:00:00Z,Screen Failure - nAb+
S00155,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,14.4,Black or African American,USA,SITE_001,22.88,CHOP_INTEND,2,2.39,A*12:73,None,110000000000000.0,2023-02-22T00:00:00Z,Screen Failure - nAb+
S00156,C91.00,B-ALL,CAR_T,CART-CD19,16,M,33.9,Asian,JPN,SITE_037,76.19,BM_blast_pct,3,0.0,A*18:62,Flu_Cy_lymphodepletion,2000000.0,2024-05-16T00:00:00Z,Dosed
S00157,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,41,M,38.4,White,FRA,SITE_006,7.35,Hb_g_dL,2,0.0,A*34:19,Busulfan_full,2000000.0,2023-09-02T00:00:00Z,Dosed
S00158,C91.00,B-ALL,CAR_T,CART-CD19,21,M,19.6,Not Reported,GBR,SITE_019,33.51,BM_blast_pct,3,0.0,A*02:72,Flu_Cy_lymphodepletion,10000000.0,2024-06-16T00:00:00Z,Dosed
S00159,C91.00,B-ALL,CAR_T,CART-CD19,11,M,27.4,Other,USA,SITE_030,88.12,BM_blast_pct,4,0.0,A*34:26,Flu_Cy_lymphodepletion,10000000.0,2023-09-30T00:00:00Z,Dosed
S00160,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,45,M,51.0,Hispanic or Latino,AUS,SITE_016,2.59,LDH_x_ULN,6,0.0,A*34:23,Flu_Cy_lymphodepletion,1000000.0,2024-01-17T00:00:00Z,Dosed
S00161,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,23.0,Black or African American,GBR,SITE_019,26.87,CHOP_INTEND,0,11.16,A*18:35,None,30000000000000.0,2023-07-08T00:00:00Z,Dosed
S00162,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,84,M,62.8,Hispanic or Latino,USA,SITE_023,40.69,BM_plasma_pct,2,0.0,A*31:43,Flu_Cy_lymphodepletion,2000000.0,2024-02-05T00:00:00Z,Dosed
S00163,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,46.3,Asian,USA,SITE_014,9.23,Hb_g_dL,2,0.0,A*31:92,Busulfan_full,3000000.0,2023-03-23T00:00:00Z,Dosed
S00164,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,1,F,29.5,White,ESP,SITE_005,23.33,CHOP_INTEND,1,5.8,A*16:61,None,200000000000000.0,2023-01-08T00:00:00Z,Dosed
S00165,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,39,M,39.6,White,JPN,SITE_010,19.59,BCVA_letters,2,3.31,A*02:27,None,110000000000000.0,2024-05-07T00:00:00Z,Screen Failure - nAb+
S00166,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,22,M,23.1,White,DEU,SITE_025,4.81,Hb_g_dL,2,0.0,A*10:75,Busulfan_reduced,5000000.0,2023-07-09T00:00:00Z,Dosed
S00167,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,60,M,52.0,Asian,CAN,SITE_003,3.53,LDH_x_ULN,5,0.0,A*17:88,Flu_Cy_lymphodepletion,1000000.0,2023-08-23T00:00:00Z,Dosed
S00168,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,63,F,66.1,Hispanic or Latino,FRA,SITE_004,3.98,LDH_x_ULN,4,0.0,A*27:04,Flu_Cy_lymphodepletion,1000000.0,2023-05-30T00:00:00Z,Dosed
S00169,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,28,F,30.5,Black or African American,ESP,SITE_021,6.39,Hb_g_dL,6,0.0,A*26:28,Treosulfan,3000000.0,2024-04-04T00:00:00Z,Dosed
S00170,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,5,M,22.4,White,USA,SITE_002,1.62,GMFC_MLD,2,0.0,A*30:88,Treosulfan,5000000.0,2024-02-13T00:00:00Z,Dosed
S00171,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,22,M,30.9,White,GBR,SITE_002,7.41,Hb_g_dL,2,0.0,A*21:56,Busulfan_reduced,3000000.0,2023-09-18T00:00:00Z,Dosed
S00172,D67,Hemophilia B,AAV,AAV-FIX-Padua,36,F,37.2,Other,AUS,SITE_024,1.57,FIX_pct,2,10.47,A*19:17,None,200000000000000.0,2024-03-17T00:00:00Z,Dosed
S00173,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,33,M,35.4,White,GBR,SITE_023,8.88,Hb_g_dL,3,0.0,A*03:34,Busulfan_reduced,2000000.0,2024-03-16T00:00:00Z,Dosed
S00174,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,57,M,54.4,Black or African American,DEU,SITE_005,76.85,BM_plasma_pct,3,0.0,A*31:26,Flu_Cy_lymphodepletion,1000000.0,2023-05-21T00:00:00Z,Dosed
S00175,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,F,10.4,White,GBR,SITE_029,28.0,NSAA,0,16.62,A*11:86,None,200000000000000.0,2023-09-18T00:00:00Z,Screen Failure - nAb+
S00176,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,41.0,Hispanic or Latino,ESP,SITE_038,17.87,CHOP_INTEND,0,1.63,A*13:73,None,30000000000000.0,2023-06-16T00:00:00Z,Dosed
S00177,D66,Hemophilia A,AAV,AAV-FVIII,39,M,46.1,White,USA,SITE_024,3.61,FVIII_pct,0,143.97,A*21:65,None,30000000000000.0,2023-02-20T00:00:00Z,Dosed
S00178,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,1,F,15.8,White,AUS,SITE_013,2.21,GMFC_MLD,2,0.0,A*19:46,Busulfan_full,8000000.0,2023-02-02T00:00:00Z,Dosed
S00179,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,50,M,51.4,White,ESP,SITE_011,61.35,BM_plasma_pct,3,0.0,A*14:24,Flu_Cy_lymphodepletion,2000000.0,2024-01-10T00:00:00Z,Dosed
S00180,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,59,M,61.1,Other,FRA,SITE_012,3.73,LDH_x_ULN,4,0.0,A*32:78,Flu_Cy_lymphodepletion,2000000.0,2023-02-01T00:00:00Z,Dosed
S00181,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,56,F,62.0,White,USA,SITE_004,58.1,BM_plasma_pct,2,0.0,A*05:70,Flu_Cy_lymphodepletion,10000000.0,2023-01-17T00:00:00Z,Dosed
S00182,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,54,F,53.5,Black or African American,FRA,SITE_018,72.12,BM_plasma_pct,5,0.0,A*18:86,Flu_Cy_lymphodepletion,1000000.0,2023-01-20T00:00:00Z,Dosed
S00183,D67,Hemophilia B,AAV,AAV-FIX-Padua,36,M,57.7,Black or African American,FRA,SITE_017,1.75,FIX_pct,2,67.76,A*12:31,None,200000000000000.0,2024-01-09T00:00:00Z,Dosed
S00184,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,21,F,22.5,White,USA,SITE_008,8.83,Hb_g_dL,6,0.0,A*20:60,Busulfan_full,2000000.0,2023-11-24T00:00:00Z,Dosed
S00185,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,54,F,46.8,White,GBR,SITE_039,3.85,LDH_x_ULN,5,0.0,A*11:75,Flu_Cy_lymphodepletion,1000000.0,2023-09-12T00:00:00Z,Dosed
S00186,C91.00,B-ALL,CAR_T,CART-CD19,1,M,6.2,White,ITA,SITE_018,63.88,BM_blast_pct,5,0.0,A*31:61,Flu_Cy_lymphodepletion,10000000.0,2024-03-22T00:00:00Z,Dosed
S00187,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,23,M,34.9,White,USA,SITE_011,7.06,Hb_g_dL,2,0.0,A*29:49,Busulfan_reduced,5000000.0,2024-03-31T00:00:00Z,Dosed
S00188,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,1,M,23.0,White,USA,SITE_016,15.22,CHOP_INTEND,2,103.61,A*05:57,None,30000000000000.0,2023-09-26T00:00:00Z,Dosed
S00189,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,76,M,77.0,White,JPN,SITE_018,3.07,LDH_x_ULN,3,0.0,A*30:82,Flu_Cy_lymphodepletion,2000000.0,2023-10-28T00:00:00Z,Dosed
S00190,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,32.5,Black or African American,ITA,SITE_038,8.89,Hb_g_dL,3,0.0,A*01:07,Treosulfan,5000000.0,2024-01-18T00:00:00Z,Dosed
S00191,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,55,M,49.6,Hispanic or Latino,AUS,SITE_030,57.41,BM_plasma_pct,3,0.0,A*27:42,Flu_Cy_lymphodepletion,2000000.0,2024-03-05T00:00:00Z,Dosed
S00192,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,39,M,52.6,White,ITA,SITE_034,6.21,Hb_g_dL,3,0.0,A*17:10,Treosulfan,2000000.0,2023-12-26T00:00:00Z,Dosed
S00193,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,21.0,White,GBR,SITE_021,20.47,NSAA,1,36.47,A*12:76,None,200000000000000.0,2024-04-12T00:00:00Z,Dosed
S00194,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,68,F,74.4,White,DEU,SITE_019,3.54,LDH_x_ULN,5,0.0,A*04:24,Flu_Cy_lymphodepletion,2000000.0,2023-03-23T00:00:00Z,Dosed
S00195,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,17.8,Not Reported,USA,SITE_002,24.47,NSAA,0,58.63,A*03:34,None,15000000000000.0,2024-03-31T00:00:00Z,Screen Failure - nAb+
S00196,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,F,9.3,White,GBR,SITE_016,15.73,NSAA,0,21.1,A*21:59,None,200000000000000.0,2024-03-03T00:00:00Z,Screen Failure - nAb+
S00197,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,63,F,49.6,White,FRA,SITE_023,53.79,mNIS_plus_7,2,0.0,A*12:53,None,1.0,2023-10-19T00:00:00Z,Dosed
S00198,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,50,M,53.8,White,ESP,SITE_014,41.84,BM_plasma_pct,2,0.0,A*34:52,Flu_Cy_lymphodepletion,1000000.0,2023-02-06T00:00:00Z,Dosed
S00199,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,16.6,Asian,AUS,SITE_004,26.6,NSAA,2,14.97,A*25:06,None,15000000000000.0,2024-04-01T00:00:00Z,Dosed
S00200,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,21,F,36.0,Black or African American,ITA,SITE_019,8.79,Hb_g_dL,3,0.0,A*07:94,Busulfan_full,3000000.0,2023-04-13T00:00:00Z,Dosed
S00201,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,75,F,51.8,White,ESP,SITE_001,2.62,LDH_x_ULN,3,0.0,A*12:48,Flu_Cy_lymphodepletion,10000000.0,2023-11-05T00:00:00Z,Dosed
S00202,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,M,11.9,Black or African American,GBR,SITE_027,4.32,GMFC_MLD,0,0.0,A*22:28,Treosulfan,8000000.0,2023-12-04T00:00:00Z,Dosed
S00203,D67,Hemophilia B,AAV,AAV-FIX-Padua,41,F,30.5,White,AUS,SITE_022,4.49,FIX_pct,1,2.09,A*24:40,None,30000000000000.0,2023-04-09T00:00:00Z,Dosed
S00204,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,1,F,26.6,Black or African American,USA,SITE_012,20.25,NSAA,1,0.28,A*02:71,None,200000000000000.0,2023-10-08T00:00:00Z,Dosed
S00205,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,7,M,20.7,White,USA,SITE_015,33.6,CHOP_INTEND,1,94.72,A*18:93,None,110000000000000.0,2023-05-02T00:00:00Z,Dosed
S00206,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,21.5,Asian,GBR,SITE_023,8.43,Hb_g_dL,2,0.0,A*31:94,Busulfan_full,3000000.0,2023-04-14T00:00:00Z,Dosed
S00207,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,F,21.7,Black or African American,USA,SITE_026,25.47,NSAA,0,282.9,A*07:04,None,15000000000000.0,2024-01-04T00:00:00Z,Screen Failure - nAb+
S00208,C91.00,B-ALL,CAR_T,CART-CD19,18,F,23.3,White,ITA,SITE_038,85.91,BM_blast_pct,2,0.0,A*19:77,Flu_Cy_lymphodepletion,5000000.0,2024-04-20T00:00:00Z,Dosed
S00209,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,M,4.0,White,FRA,SITE_013,16.04,NSAA,2,1.4,A*32:54,None,60000000000000.0,2023-04-27T00:00:00Z,Dosed
S00210,D67,Hemophilia B,AAV,AAV-FIX-Padua,29,F,40.6,Black or African American,GBR,SITE_037,1.6,FIX_pct,2,16.74,A*32:93,None,60000000000000.0,2023-05-18T00:00:00Z,Dosed
S00211,C91.00,B-ALL,CAR_T,CART-CD19,1,F,21.8,White,ITA,SITE_002,63.06,BM_blast_pct,6,0.0,A*06:77,Flu_Cy_lymphodepletion,1000000.0,2023-07-23T00:00:00Z,Dosed
S00212,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,63,M,60.0,White,FRA,SITE_014,49.99,mNIS_plus_7,0,0.0,A*18:87,None,0.3,2023-01-26T00:00:00Z,Dosed
S00213,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,M,10.3,White,CAN,SITE_010,23.01,NSAA,1,0.34,A*12:28,None,30000000000000.0,2024-01-10T00:00:00Z,Dosed
S00214,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,68,M,70.7,White,JPN,SITE_025,3.03,LDH_x_ULN,2,0.0,A*26:25,Flu_Cy_lymphodepletion,5000000.0,2024-01-01T00:00:00Z,Dosed
S00215,C91.00,B-ALL,CAR_T,CART-CD19,9,M,35.0,Black or African American,ITA,SITE_004,26.03,BM_blast_pct,6,0.0,A*23:55,Flu_Cy_lymphodepletion,5000000.0,2024-02-10T00:00:00Z,Dosed
S00216,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,79,M,56.6,Black or African American,JPN,SITE_035,1.37,LDH_x_ULN,2,0.0,A*32:38,Flu_Cy_lymphodepletion,1000000.0,2023-06-04T00:00:00Z,Dosed
S00217,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,7,M,19.3,White,AUS,SITE_035,16.32,NSAA,1,36.88,A*03:40,None,60000000000000.0,2024-02-19T00:00:00Z,Screen Failure - nAb+
S00218,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,26.2,Hispanic or Latino,FRA,SITE_004,19.7,NSAA,2,14.47,A*33:43,None,30000000000000.0,2024-03-27T00:00:00Z,Dosed
S00219,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,71,F,60.8,White,ESP,SITE_019,41.63,BM_plasma_pct,5,0.0,A*27:66,Flu_Cy_lymphodepletion,1000000.0,2023-07-09T00:00:00Z,Dosed
S00220,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,21,F,13.0,Asian,USA,SITE_011,5.98,Hb_g_dL,3,0.0,A*07:37,Treosulfan,3000000.0,2024-03-20T00:00:00Z,Dosed
S00221,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,25,F,43.1,White,ITA,SITE_038,8.28,Hb_g_dL,2,0.0,A*15:70,Busulfan_reduced,3000000.0,2023-07-05T00:00:00Z,Dosed
S00222,D67,Hemophilia B,AAV,AAV-FIX-Padua,40,M,48.1,White,AUS,SITE_036,3.52,FIX_pct,2,2.36,A*18:24,None,30000000000000.0,2023-11-29T00:00:00Z,Screen Failure - nAb+
S00223,C91.00,B-ALL,CAR_T,CART-CD19,22,M,38.1,Asian,USA,SITE_040,81.09,BM_blast_pct,4,0.0,A*10:29,Flu_Cy_lymphodepletion,10000000.0,2024-04-21T00:00:00Z,Dosed
S00224,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,6,F,24.2,Hispanic or Latino,USA,SITE_040,2.52,GMFC_MLD,0,0.0,A*28:39,Treosulfan,3000000.0,2023-09-02T00:00:00Z,Dosed
S00225,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,33,M,22.8,White,JPN,SITE_010,9.36,Hb_g_dL,5,0.0,A*14:90,Busulfan_reduced,3000000.0,2023-05-13T00:00:00Z,Dosed
S00226,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,51,F,49.1,White,JPN,SITE_023,53.36,BM_plasma_pct,3,0.0,A*21:56,Flu_Cy_lymphodepletion,2000000.0,2023-06-04T00:00:00Z,Dosed
S00227,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,0,F,14.9,White,DEU,SITE_032,28.64,CHOP_INTEND,2,2.83,A*23:79,None,30000000000000.0,2024-04-05T00:00:00Z,Screen Failure - nAb+
S00228,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,33,F,36.9,Asian,GBR,SITE_010,33.5,BCVA_letters,0,8.38,A*09:17,None,60000000000000.0,2023-07-29T00:00:00Z,Dosed
S00229,C91.00,B-ALL,CAR_T,CART-CD19,12,F,33.1,White,DEU,SITE_038,81.6,BM_blast_pct,3,0.0,A*29:68,Flu_Cy_lymphodepletion,5000000.0,2023-10-15T00:00:00Z,Dosed
S00230,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,9.4,White,FRA,SITE_036,15.75,CHOP_INTEND,1,11.11,A*06:79,None,60000000000000.0,2023-02-09T00:00:00Z,Screen Failure - nAb+
S00231,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,0,F,8.4,White,USA,SITE_022,14.17,NSAA,2,1.95,A*18:51,None,60000000000000.0,2024-03-12T00:00:00Z,Dosed
S00232,D66,Hemophilia A,AAV,AAV-FVIII,22,M,27.6,Asian,AUS,SITE_032,1.55,FVIII_pct,0,5.05,A*14:89,None,110000000000000.0,2024-01-18T00:00:00Z,Screen Failure - nAb+
S00233,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,5,M,14.8,White,GBR,SITE_032,3.18,GMFC_MLD,0,0.0,A*09:70,Busulfan_full,5000000.0,2024-06-18T00:00:00Z,Dosed
S00234,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,67,M,60.1,White,USA,SITE_019,46.5,mNIS_plus_7,2,0.0,A*27:19,None,1.0,2023-09-26T00:00:00Z,Dosed
S00235,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,59,M,41.0,Hispanic or Latino,USA,SITE_004,74.1,BM_plasma_pct,4,0.0,A*28:89,Flu_Cy_lymphodepletion,10000000.0,2023-10-02T00:00:00Z,Dosed
S00236,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,67,M,65.0,Hispanic or Latino,ESP,SITE_025,1.95,LDH_x_ULN,2,0.0,A*01:08,Flu_Cy_lymphodepletion,5000000.0,2024-05-25T00:00:00Z,Dosed
S00237,D66,Hemophilia A,AAV,AAV-FVIII,37,F,44.1,Not Reported,GBR,SITE_007,4.2,FVIII_pct,0,19.87,A*31:22,None,15000000000000.0,2023-11-22T00:00:00Z,Screen Failure - nAb+
S00238,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,60,M,57.9,White,GBR,SITE_020,1.31,LDH_x_ULN,2,0.0,A*04:63,Flu_Cy_lymphodepletion,1000000.0,2023-07-09T00:00:00Z,Dosed
S00239,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,0,F,10.3,White,ITA,SITE_038,19.64,CHOP_INTEND,1,1.26,A*29:46,None,15000000000000.0,2023-05-01T00:00:00Z,Dosed
S00240,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,7,F,19.7,White,CAN,SITE_022,29.26,CHOP_INTEND,2,230.8,A*01:49,None,15000000000000.0,2023-02-03T00:00:00Z,Dosed
S00241,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,69,M,49.1,White,ITA,SITE_030,1.55,LDH_x_ULN,6,0.0,A*06:03,Flu_Cy_lymphodepletion,1000000.0,2023-04-19T00:00:00Z,Dosed
S00242,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,49,M,46.2,Black or African American,AUS,SITE_021,2.79,LDH_x_ULN,3,0.0,A*09:43,Flu_Cy_lymphodepletion,1000000.0,2024-05-13T00:00:00Z,Dosed
S00243,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,24,F,38.8,Other,CAN,SITE_040,8.96,Hb_g_dL,2,0.0,A*16:25,Busulfan_full,5000000.0,2024-03-14T00:00:00Z,Dosed
S00244,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,0,M,21.6,White,USA,SITE_034,33.93,BCVA_letters,1,5.88,A*22:49,None,200000000000000.0,2023-10-10T00:00:00Z,Dosed
S00245,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,68,F,66.3,White,DEU,SITE_031,46.75,mNIS_plus_7,0,0.0,A*13:58,None,1.0,2023-05-06T00:00:00Z,Dosed
S00246,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,66,F,61.3,White,GBR,SITE_018,70.75,BM_plasma_pct,4,0.0,A*11:53,Flu_Cy_lymphodepletion,10000000.0,2023-05-28T00:00:00Z,Dosed
S00247,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,59,M,61.7,White,CAN,SITE_028,55.42,mNIS_plus_7,1,0.0,A*18:11,None,0.3,2023-08-13T00:00:00Z,Dosed
S00248,D66,Hemophilia A,AAV,AAV-FVIII,46,M,39.3,Other,USA,SITE_002,3.49,FVIII_pct,2,10.91,A*16:43,None,200000000000000.0,2024-05-12T00:00:00Z,Screen Failure - nAb+
S00249,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,16,M,22.8,White,USA,SITE_022,4.65,Hb_g_dL,2,0.0,A*07:10,Busulfan_full,3000000.0,2023-06-16T00:00:00Z,Dosed
S00250,D66,Hemophilia A,AAV,AAV-FVIII,45,M,48.9,Other,GBR,SITE_016,1.51,FVIII_pct,0,6.28,A*31:97,None,30000000000000.0,2023-11-30T00:00:00Z,Screen Failure - nAb+
S00251,C91.00,B-ALL,CAR_T,CART-CD19,1,F,8.4,Not Reported,DEU,SITE_009,65.5,BM_blast_pct,4,0.0,A*15:13,Flu_Cy_lymphodepletion,2000000.0,2023-08-25T00:00:00Z,Dosed
S00252,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,64,F,60.4,Black or African American,CAN,SITE_012,32.88,BM_plasma_pct,6,0.0,A*14:91,Flu_Cy_lymphodepletion,2000000.0,2023-11-03T00:00:00Z,Dosed
S00253,D66,Hemophilia A,AAV,AAV-FVIII,22,M,25.4,Black or African American,USA,SITE_019,1.62,FVIII_pct,2,50.19,A*09:86,None,110000000000000.0,2023-05-31T00:00:00Z,Dosed
S00254,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,36,M,41.2,Black or African American,ESP,SITE_025,8.36,Hb_g_dL,2,0.0,A*09:68,Busulfan_reduced,3000000.0,2023-09-14T00:00:00Z,Dosed
S00255,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,27.5,Black or African American,DEU,SITE_029,8.67,Hb_g_dL,6,0.0,A*27:47,Treosulfan,2000000.0,2024-01-20T00:00:00Z,Dosed
S00256,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,39,M,24.4,White,USA,SITE_006,1.51,LDH_x_ULN,6,0.0,A*23:28,Flu_Cy_lymphodepletion,5000000.0,2023-08-14T00:00:00Z,Dosed
S00257,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,72,F,74.5,Hispanic or Latino,CAN,SITE_007,3.33,LDH_x_ULN,2,0.0,A*06:46,Flu_Cy_lymphodepletion,10000000.0,2024-03-05T00:00:00Z,Dosed
S00258,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,15.6,White,FRA,SITE_028,29.93,CHOP_INTEND,2,2.92,A*31:10,None,15000000000000.0,2023-11-16T00:00:00Z,Screen Failure - nAb+
S00259,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,24.3,White,USA,SITE_023,14.58,CHOP_INTEND,0,4.17,A*16:25,None,110000000000000.0,2023-05-22T00:00:00Z,Dosed
S00260,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,64,F,64.2,Black or African American,CAN,SITE_009,100.01,mNIS_plus_7,2,0.0,A*06:61,None,1.0,2023-05-31T00:00:00Z,Dosed
S00261,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,7,F,34.5,White,FRA,SITE_003,21.68,NSAA,2,1.24,A*06:60,None,15000000000000.0,2024-05-16T00:00:00Z,Dosed
S00262,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,72,M,67.6,White,AUS,SITE_033,1.63,LDH_x_ULN,5,0.0,A*30:96,Flu_Cy_lymphodepletion,10000000.0,2023-02-22T00:00:00Z,Dosed
S00263,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,31,F,14.8,Asian,USA,SITE_004,9.1,Hb_g_dL,5,0.0,A*21:53,Busulfan_full,2000000.0,2023-02-12T00:00:00Z,Dosed
S00264,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,16.7,Asian,DEU,SITE_028,17.9,NSAA,2,37.98,A*25:25,None,110000000000000.0,2023-11-11T00:00:00Z,Dosed
S00265,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,58,F,38.6,Black or African American,GBR,SITE_008,37.06,BM_plasma_pct,3,0.0,A*14:27,Flu_Cy_lymphodepletion,10000000.0,2024-04-09T00:00:00Z,Dosed
S00266,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,1,M,18.1,White,DEU,SITE_011,17.22,NSAA,0,2.85,A*34:71,None,15000000000000.0,2024-05-07T00:00:00Z,Dosed
S00267,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,31,F,36.5,Hispanic or Latino,USA,SITE_027,7.79,Hb_g_dL,5,0.0,A*14:74,Busulfan_full,5000000.0,2023-04-05T00:00:00Z,Dosed
S00268,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,F,35.5,Hispanic or Latino,FRA,SITE_020,23.08,NSAA,0,10.62,A*21:61,None,60000000000000.0,2023-09-25T00:00:00Z,Screen Failure - nAb+
S00269,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,M,31.9,White,USA,SITE_024,21.05,CHOP_INTEND,0,6.8,A*09:32,None,200000000000000.0,2023-02-08T00:00:00Z,Screen Failure - nAb+
S00270,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,35.0,White,DEU,SITE_013,34.1,CHOP_INTEND,0,19.35,A*19:71,None,110000000000000.0,2024-04-14T00:00:00Z,Dosed
S00271,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,4.0,Black or African American,JPN,SITE_011,15.55,CHOP_INTEND,0,4.51,A*04:30,None,15000000000000.0,2024-03-18T00:00:00Z,Screen Failure - nAb+
S00272,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,13.5,White,JPN,SITE_032,26.25,NSAA,2,3.51,A*07:84,None,200000000000000.0,2024-06-04T00:00:00Z,Dosed
S00273,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,7,M,13.8,White,ITA,SITE_011,14.25,CHOP_INTEND,2,1.1,A*33:06,None,60000000000000.0,2024-01-17T00:00:00Z,Dosed
S00274,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,63,F,49.3,Black or African American,JPN,SITE_018,105.02,mNIS_plus_7,0,0.0,A*10:30,None,0.7,2023-05-18T00:00:00Z,Dosed
S00275,C91.00,B-ALL,CAR_T,CART-CD19,5,F,28.6,Black or African American,USA,SITE_007,68.77,BM_blast_pct,6,0.0,A*10:98,Flu_Cy_lymphodepletion,2000000.0,2023-12-18T00:00:00Z,Dosed
S00276,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,26,M,44.6,White,USA,SITE_028,6.17,Hb_g_dL,2,0.0,A*09:13,Busulfan_reduced,5000000.0,2024-01-31T00:00:00Z,Dosed
S00277,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,18,F,22.2,White,CAN,SITE_011,9.04,Hb_g_dL,5,0.0,A*20:83,Busulfan_reduced,2000000.0,2023-02-08T00:00:00Z,Dosed
S00278,D67,Hemophilia B,AAV,AAV-FIX-Padua,35,M,43.0,Not Reported,JPN,SITE_003,4.31,FIX_pct,0,9.88,A*02:73,None,110000000000000.0,2024-01-20T00:00:00Z,Dosed
S00279,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,77,M,68.8,Black or African American,GBR,SITE_015,36.19,BM_plasma_pct,3,0.0,A*07:48,Flu_Cy_lymphodepletion,2000000.0,2023-01-25T00:00:00Z,Dosed
S00280,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,55,F,59.4,Not Reported,USA,SITE_005,37.13,BM_plasma_pct,6,0.0,A*02:71,Flu_Cy_lymphodepletion,1000000.0,2023-11-21T00:00:00Z,Dosed
S00281,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,10.1,White,JPN,SITE_025,34.66,CHOP_INTEND,1,123.78,A*23:55,None,60000000000000.0,2023-09-16T00:00:00Z,Dosed
S00282,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,F,24.8,White,ESP,SITE_002,27.12,NSAA,1,8.89,A*28:49,None,60000000000000.0,2023-04-04T00:00:00Z,Dosed
S00283,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,24,M,44.7,Hispanic or Latino,USA,SITE_006,7.15,Hb_g_dL,3,0.0,A*07:60,Busulfan_full,2000000.0,2023-10-26T00:00:00Z,Dosed
S00284,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,24.9,Black or African American,ITA,SITE_004,6.62,Hb_g_dL,4,0.0,A*32:53,Treosulfan,2000000.0,2024-05-13T00:00:00Z,Dosed
S00285,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,58,F,60.9,White,USA,SITE_001,35.01,mNIS_plus_7,0,0.0,A*04:97,None,0.1,2023-12-05T00:00:00Z,Dosed
S00286,D66,Hemophilia A,AAV,AAV-FVIII,47,F,63.7,White,GBR,SITE_035,2.42,FVIII_pct,2,5.37,A*28:28,None,110000000000000.0,2023-06-28T00:00:00Z,Dosed
S00287,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,F,16.9,Black or African American,USA,SITE_006,30.2,CHOP_INTEND,2,13.28,A*24:29,None,15000000000000.0,2023-07-06T00:00:00Z,Screen Failure - nAb+
S00288,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,15,M,23.4,White,FRA,SITE_021,4.53,Hb_g_dL,2,0.0,A*16:94,Busulfan_full,2000000.0,2023-05-12T00:00:00Z,Dosed
S00289,D67,Hemophilia B,AAV,AAV-FIX-Padua,27,F,26.9,Hispanic or Latino,GBR,SITE_032,1.46,FIX_pct,0,32.78,A*11:34,None,200000000000000.0,2024-03-09T00:00:00Z,Dosed
S00290,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,4.0,Black or African American,DEU,SITE_011,22.22,CHOP_INTEND,2,1.86,A*02:09,None,110000000000000.0,2024-03-13T00:00:00Z,Screen Failure - nAb+
S00291,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,68,M,51.7,Black or African American,GBR,SITE_012,2.43,LDH_x_ULN,2,0.0,A*29:34,Flu_Cy_lymphodepletion,1000000.0,2023-05-04T00:00:00Z,Dosed
S00292,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,F,7.0,White,CAN,SITE_039,24.87,CHOP_INTEND,0,31.02,A*22:56,None,15000000000000.0,2023-10-27T00:00:00Z,Dosed
S00293,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,75,M,76.3,White,AUS,SITE_026,31.68,BM_plasma_pct,5,0.0,A*02:28,Flu_Cy_lymphodepletion,1000000.0,2023-02-20T00:00:00Z,Dosed
S00294,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,F,15.9,White,USA,SITE_004,20.83,CHOP_INTEND,1,1.17,A*12:72,None,30000000000000.0,2023-10-22T00:00:00Z,Screen Failure - nAb+
S00295,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,74,F,67.5,White,FRA,SITE_035,1.08,LDH_x_ULN,4,0.0,A*05:93,Flu_Cy_lymphodepletion,2000000.0,2023-06-22T00:00:00Z,Dosed
S00296,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,61,F,47.3,White,CAN,SITE_003,31.28,BM_plasma_pct,4,0.0,A*21:32,Flu_Cy_lymphodepletion,1000000.0,2023-03-04T00:00:00Z,Dosed
S00297,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,M,25.9,White,CAN,SITE_020,4.42,GMFC_MLD,0,0.0,A*30:10,Busulfan_full,3000000.0,2024-03-03T00:00:00Z,Dosed
S00298,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,65,M,63.2,Asian,GBR,SITE_023,3.54,LDH_x_ULN,5,0.0,A*32:40,Flu_Cy_lymphodepletion,1000000.0,2024-04-03T00:00:00Z,Dosed
S00299,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,61,M,65.4,White,ESP,SITE_002,1.73,LDH_x_ULN,4,0.0,A*13:19,Flu_Cy_lymphodepletion,2000000.0,2023-06-30T00:00:00Z,Dosed
S00300,C91.00,B-ALL,CAR_T,CART-CD19,12,M,26.0,White,FRA,SITE_030,35.24,BM_blast_pct,6,0.0,A*07:11,Flu_Cy_lymphodepletion,5000000.0,2023-09-29T00:00:00Z,Dosed
S00301,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,F,64.3,Asian,GBR,SITE_016,1.1,LDH_x_ULN,4,0.0,A*04:88,Flu_Cy_lymphodepletion,1000000.0,2023-01-13T00:00:00Z,Dosed
S00302,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,0,M,11.8,White,GBR,SITE_023,23.34,NSAA,2,45.89,A*07:34,None,200000000000000.0,2023-11-12T00:00:00Z,Screen Failure - nAb+
S00303,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,5,M,15.3,Black or African American,GBR,SITE_026,14.73,BCVA_letters,1,16.05,A*15:52,None,110000000000000.0,2024-04-13T00:00:00Z,Screen Failure - nAb+
S00304,D67,Hemophilia B,AAV,AAV-FIX-Padua,40,M,39.5,White,AUS,SITE_027,2.82,FIX_pct,2,27.53,A*02:29,None,110000000000000.0,2024-04-12T00:00:00Z,Screen Failure - nAb+
S00305,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,68,F,68.2,Black or African American,CAN,SITE_022,77.23,BM_plasma_pct,4,0.0,A*15:14,Flu_Cy_lymphodepletion,2000000.0,2024-04-19T00:00:00Z,Dosed
S00306,D66,Hemophilia A,AAV,AAV-FVIII,48,F,47.3,Asian,USA,SITE_035,1.3,FVIII_pct,2,0.78,A*03:68,None,30000000000000.0,2023-12-16T00:00:00Z,Screen Failure - nAb+
S00307,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,29,F,37.6,Hispanic or Latino,USA,SITE_036,7.25,Hb_g_dL,4,0.0,A*18:37,Busulfan_full,5000000.0,2023-10-01T00:00:00Z,Dosed
S00308,C91.00,B-ALL,CAR_T,CART-CD19,1,F,16.1,White,FRA,SITE_003,44.47,BM_blast_pct,5,0.0,A*08:43,Flu_Cy_lymphodepletion,5000000.0,2023-02-04T00:00:00Z,Dosed
S00309,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,28,F,40.9,White,JPN,SITE_011,7.61,Hb_g_dL,5,0.0,A*12:16,Busulfan_reduced,3000000.0,2024-01-01T00:00:00Z,Dosed
S00310,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,24.4,Black or African American,USA,SITE_008,27.78,NSAA,1,3.1,A*06:56,None,60000000000000.0,2023-06-27T00:00:00Z,Screen Failure - nAb+
S00311,D66,Hemophilia A,AAV,AAV-FVIII,36,M,22.1,White,JPN,SITE_008,1.16,FVIII_pct,2,7.71,A*13:15,None,200000000000000.0,2023-01-12T00:00:00Z,Screen Failure - nAb+
S00312,D66,Hemophilia A,AAV,AAV-FVIII,36,M,27.9,Black or African American,ESP,SITE_033,1.0,FVIII_pct,1,3.15,A*06:98,None,15000000000000.0,2024-02-27T00:00:00Z,Dosed
S00313,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,13,F,25.9,Asian,USA,SITE_019,9.16,Hb_g_dL,3,0.0,A*01:38,Busulfan_full,5000000.0,2024-02-10T00:00:00Z,Dosed
S00314,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,17,F,22.8,White,JPN,SITE_039,5.76,Hb_g_dL,4,0.0,A*16:78,Busulfan_reduced,3000000.0,2023-08-10T00:00:00Z,Dosed
S00315,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,13,M,9.2,Hispanic or Latino,USA,SITE_038,6.26,Hb_g_dL,3,0.0,A*16:34,Treosulfan,2000000.0,2024-03-28T00:00:00Z,Dosed
S00316,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,36.8,White,ITA,SITE_020,8.35,Hb_g_dL,6,0.0,A*01:94,Treosulfan,3000000.0,2023-11-26T00:00:00Z,Dosed
S00317,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,23,F,22.3,Asian,GBR,SITE_016,7.42,Hb_g_dL,6,0.0,A*15:96,Busulfan_reduced,3000000.0,2023-01-01T00:00:00Z,Dosed
S00318,C91.00,B-ALL,CAR_T,CART-CD19,11,F,14.9,White,DEU,SITE_033,69.29,BM_blast_pct,4,0.0,A*10:51,Flu_Cy_lymphodepletion,10000000.0,2023-11-22T00:00:00Z,Dosed
S00319,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,20.7,Asian,ESP,SITE_037,6.69,Hb_g_dL,5,0.0,A*03:54,Treosulfan,5000000.0,2023-10-13T00:00:00Z,Dosed
S00320,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,7,M,20.3,White,FRA,SITE_040,0.65,GMFC_MLD,1,0.0,A*32:16,Busulfan_reduced,8000000.0,2024-06-06T00:00:00Z,Dosed
S00321,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,55,M,40.8,White,FRA,SITE_026,69.77,BM_plasma_pct,5,0.0,A*21:23,Flu_Cy_lymphodepletion,5000000.0,2023-11-16T00:00:00Z,Dosed
S00322,D67,Hemophilia B,AAV,AAV-FIX-Padua,37,M,39.1,White,FRA,SITE_036,1.9,FIX_pct,0,1.07,A*12:42,None,30000000000000.0,2024-06-10T00:00:00Z,Screen Failure - nAb+
S00323,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,34,F,50.2,Black or African American,CAN,SITE_012,8.08,Hb_g_dL,3,0.0,A*10:29,Busulfan_full,5000000.0,2024-05-22T00:00:00Z,Dosed
S00324,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,40,F,41.2,Black or African American,FRA,SITE_025,41.66,BCVA_letters,1,25.66,A*10:96,None,200000000000000.0,2024-03-14T00:00:00Z,Dosed
S00325,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,72,M,71.3,White,USA,SITE_031,1.42,LDH_x_ULN,3,0.0,A*11:88,Flu_Cy_lymphodepletion,2000000.0,2023-06-02T00:00:00Z,Dosed
S00326,C91.00,B-ALL,CAR_T,CART-CD19,13,F,23.8,Asian,GBR,SITE_007,74.77,BM_blast_pct,2,0.0,A*22:78,Flu_Cy_lymphodepletion,5000000.0,2023-08-05T00:00:00Z,Dosed
S00327,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,77,F,59.4,White,USA,SITE_020,3.34,LDH_x_ULN,3,0.0,A*10:44,Flu_Cy_lymphodepletion,10000000.0,2023-02-02T00:00:00Z,Dosed
S00328,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,39,M,37.3,Not Reported,GBR,SITE_023,40.9,BCVA_letters,2,12.18,A*09:43,None,15000000000000.0,2023-06-04T00:00:00Z,Dosed
S00329,C91.00,B-ALL,CAR_T,CART-CD19,11,M,28.0,Other,JPN,SITE_001,34.31,BM_blast_pct,3,0.0,A*09:61,Flu_Cy_lymphodepletion,1000000.0,2023-05-17T00:00:00Z,Dosed
S00330,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,25,M,20.2,Hispanic or Latino,USA,SITE_037,8.78,Hb_g_dL,5,0.0,A*15:36,Busulfan_reduced,2000000.0,2024-03-30T00:00:00Z,Dosed
S00331,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,45,F,43.8,White,GBR,SITE_006,3.01,LDH_x_ULN,6,0.0,A*12:55,Flu_Cy_lymphodepletion,10000000.0,2024-04-22T00:00:00Z,Dosed
S00332,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,12.6,White,JPN,SITE_039,22.38,NSAA,2,2.61,A*15:30,None,110000000000000.0,2023-11-03T00:00:00Z,Dosed
S00333,C91.00,B-ALL,CAR_T,CART-CD19,1,F,13.7,White,AUS,SITE_029,78.03,BM_blast_pct,2,0.0,A*23:18,Flu_Cy_lymphodepletion,2000000.0,2023-01-28T00:00:00Z,Dosed
S00334,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,63,M,57.7,White,DEU,SITE_035,44.87,BM_plasma_pct,6,0.0,A*08:90,Flu_Cy_lymphodepletion,2000000.0,2023-10-19T00:00:00Z,Dosed
S00335,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,21.4,White,USA,SITE_027,14.8,NSAA,2,0.52,A*32:90,None,30000000000000.0,2024-04-25T00:00:00Z,Dosed
S00336,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,68,M,67.8,White,GBR,SITE_006,60.4,mNIS_plus_7,0,0.0,A*20:87,None,0.3,2024-04-01T00:00:00Z,Dosed
S00337,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,13.4,Hispanic or Latino,ITA,SITE_015,24.29,CHOP_INTEND,0,13.84,A*30:06,None,110000000000000.0,2024-02-03T00:00:00Z,Dosed
S00338,C91.00,B-ALL,CAR_T,CART-CD19,8,M,6.4,White,JPN,SITE_004,47.62,BM_blast_pct,3,0.0,A*33:60,Flu_Cy_lymphodepletion,5000000.0,2023-07-09T00:00:00Z,Dosed
S00339,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,F,30.2,White,DEU,SITE_010,20.59,CHOP_INTEND,2,2.53,A*21:05,None,30000000000000.0,2023-01-14T00:00:00Z,Screen Failure - nAb+
S00340,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,39,F,51.8,White,USA,SITE_007,46.56,BM_plasma_pct,3,0.0,A*23:80,Flu_Cy_lymphodepletion,2000000.0,2024-04-21T00:00:00Z,Dosed
S00341,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,35.4,Asian,JPN,SITE_036,25.65,NSAA,2,17.87,A*14:79,None,60000000000000.0,2024-05-19T00:00:00Z,Dosed
S00342,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,F,15.0,Hispanic or Latino,USA,SITE_018,4.92,GMFC_MLD,2,0.0,A*28:84,Treosulfan,5000000.0,2023-05-15T00:00:00Z,Dosed
S00343,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,81,F,66.5,Hispanic or Latino,DEU,SITE_023,2.74,LDH_x_ULN,6,0.0,A*06:72,Flu_Cy_lymphodepletion,10000000.0,2023-04-29T00:00:00Z,Dosed
S00344,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,75,F,74.3,White,USA,SITE_019,98.52,mNIS_plus_7,0,0.0,A*28:51,None,0.1,2023-02-18T00:00:00Z,Dosed
S00345,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,51,M,50.8,White,ITA,SITE_009,1.25,LDH_x_ULN,5,0.0,A*18:75,Flu_Cy_lymphodepletion,2000000.0,2023-03-27T00:00:00Z,Dosed
S00346,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,48,M,49.7,White,JPN,SITE_001,1.5,LDH_x_ULN,6,0.0,A*06:97,Flu_Cy_lymphodepletion,2000000.0,2023-06-26T00:00:00Z,Dosed
S00347,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,7,M,24.8,Asian,AUS,SITE_021,2.02,GMFC_MLD,0,0.0,A*23:29,Busulfan_reduced,5000000.0,2024-05-22T00:00:00Z,Dosed
S00348,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,13.7,Asian,GBR,SITE_020,8.82,Hb_g_dL,5,0.0,A*03:80,Treosulfan,2000000.0,2024-06-03T00:00:00Z,Dosed
S00349,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,53,F,45.8,White,GBR,SITE_021,104.23,mNIS_plus_7,0,0.0,A*33:52,None,0.1,2024-05-15T00:00:00Z,Dosed
S00350,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,M,20.6,White,GBR,SITE_034,24.06,CHOP_INTEND,0,6.06,A*19:64,None,30000000000000.0,2024-02-25T00:00:00Z,Dosed
S00351,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,69,M,63.9,White,USA,SITE_013,44.26,mNIS_plus_7,0,0.0,A*01:05,None,0.1,2023-09-02T00:00:00Z,Dosed
S00352,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,25.3,Black or African American,ESP,SITE_034,21.9,NSAA,0,10.17,A*25:43,None,200000000000000.0,2023-07-30T00:00:00Z,Dosed
S00353,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,34,M,44.4,Hispanic or Latino,ITA,SITE_031,31.97,BCVA_letters,0,3.73,A*19:54,None,15000000000000.0,2023-07-18T00:00:00Z,Dosed
S00354,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,60,M,50.9,Black or African American,FRA,SITE_025,79.67,mNIS_plus_7,1,0.0,A*27:41,None,0.7,2023-09-11T00:00:00Z,Dosed
S00355,D66,Hemophilia A,AAV,AAV-FVIII,45,M,56.9,White,JPN,SITE_032,2.13,FVIII_pct,1,5.37,A*24:51,None,15000000000000.0,2023-02-08T00:00:00Z,Dosed
S00356,D67,Hemophilia B,AAV,AAV-FIX-Padua,33,F,41.3,White,ITA,SITE_003,2.7,FIX_pct,0,11.29,A*32:36,None,60000000000000.0,2023-07-31T00:00:00Z,Dosed
S00357,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,76,M,71.8,White,ESP,SITE_029,1.24,LDH_x_ULN,2,0.0,A*16:80,Flu_Cy_lymphodepletion,1000000.0,2024-04-24T00:00:00Z,Dosed
S00358,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,75,F,60.2,Black or African American,ESP,SITE_001,2.86,LDH_x_ULN,3,0.0,A*23:46,Flu_Cy_lymphodepletion,1000000.0,2023-07-20T00:00:00Z,Dosed
S00359,D67,Hemophilia B,AAV,AAV-FIX-Padua,23,M,45.7,Not Reported,ESP,SITE_017,1.01,FIX_pct,0,3.71,A*33:80,None,30000000000000.0,2023-07-12T00:00:00Z,Dosed
S00360,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,61,F,45.9,Not Reported,ESP,SITE_010,108.95,mNIS_plus_7,0,0.0,A*03:84,None,1.0,2024-05-16T00:00:00Z,Dosed
S00361,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,61,M,51.7,White,ESP,SITE_021,76.23,BM_plasma_pct,6,0.0,A*22:73,Flu_Cy_lymphodepletion,2000000.0,2023-01-21T00:00:00Z,Dosed
S00362,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,19.2,Asian,DEU,SITE_031,23.26,CHOP_INTEND,2,36.9,A*04:80,None,30000000000000.0,2024-04-20T00:00:00Z,Dosed
S00363,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,F,15.4,White,JPN,SITE_035,19.66,CHOP_INTEND,1,4.66,A*14:40,None,30000000000000.0,2024-05-12T00:00:00Z,Dosed
S00364,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,8.8,Hispanic or Latino,FRA,SITE_007,33.07,CHOP_INTEND,1,2.5,A*11:55,None,200000000000000.0,2023-10-17T00:00:00Z,Screen Failure - nAb+
S00365,C91.00,B-ALL,CAR_T,CART-CD19,16,M,23.7,White,JPN,SITE_024,58.16,BM_blast_pct,5,0.0,A*02:60,Flu_Cy_lymphodepletion,2000000.0,2023-02-07T00:00:00Z,Dosed
S00366,D66,Hemophilia A,AAV,AAV-FVIII,18,F,49.5,White,USA,SITE_015,1.74,FVIII_pct,0,2.61,A*12:60,None,60000000000000.0,2023-04-07T00:00:00Z,Dosed
S00367,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,63,M,49.9,Hispanic or Latino,AUS,SITE_012,2.28,LDH_x_ULN,3,0.0,A*33:62,Flu_Cy_lymphodepletion,10000000.0,2024-02-10T00:00:00Z,Dosed
S00368,C91.00,B-ALL,CAR_T,CART-CD19,25,F,23.8,Other,ESP,SITE_027,50.74,BM_blast_pct,2,0.0,A*12:31,Flu_Cy_lymphodepletion,5000000.0,2023-03-12T00:00:00Z,Dosed
S00369,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,13.7,White,DEU,SITE_020,6.63,Hb_g_dL,2,0.0,A*15:07,Busulfan_full,3000000.0,2024-05-30T00:00:00Z,Dosed
S00370,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,65,M,71.8,White,ITA,SITE_009,32.74,BM_plasma_pct,5,0.0,A*05:68,Flu_Cy_lymphodepletion,2000000.0,2024-06-06T00:00:00Z,Dosed
S00371,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,M,45.9,White,ESP,SITE_001,1.22,LDH_x_ULN,3,0.0,A*15:22,Flu_Cy_lymphodepletion,1000000.0,2023-09-10T00:00:00Z,Dosed
S00372,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,F,18.3,White,ESP,SITE_004,7.29,Hb_g_dL,2,0.0,A*09:24,Busulfan_full,5000000.0,2023-02-21T00:00:00Z,Dosed
S00373,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,44,M,37.4,Black or African American,USA,SITE_015,7.41,Hb_g_dL,4,0.0,A*09:30,Busulfan_reduced,3000000.0,2023-04-10T00:00:00Z,Dosed
S00374,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,20.9,Black or African American,GBR,SITE_011,6.69,Hb_g_dL,2,0.0,A*32:54,Busulfan_full,3000000.0,2023-11-02T00:00:00Z,Dosed
S00375,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,25.6,White,GBR,SITE_029,17.1,NSAA,2,1.68,A*07:42,None,60000000000000.0,2024-01-31T00:00:00Z,Dosed
S00376,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,20.9,White,JPN,SITE_026,21.15,NSAA,2,58.71,A*27:63,None,200000000000000.0,2023-10-22T00:00:00Z,Screen Failure - nAb+
S00377,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,51,M,60.6,White,USA,SITE_033,52.12,BM_plasma_pct,4,0.0,A*26:69,Flu_Cy_lymphodepletion,1000000.0,2023-12-30T00:00:00Z,Dosed
S00378,D66,Hemophilia A,AAV,AAV-FVIII,63,M,55.8,White,CAN,SITE_014,3.87,FVIII_pct,1,2.55,A*07:66,None,110000000000000.0,2023-10-23T00:00:00Z,Dosed
S00379,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,14,F,35.5,White,GBR,SITE_039,5.58,Hb_g_dL,4,0.0,A*28:48,Treosulfan,5000000.0,2024-01-15T00:00:00Z,Dosed
S00380,C91.00,B-ALL,CAR_T,CART-CD19,7,F,7.4,Asian,ESP,SITE_012,70.19,BM_blast_pct,6,0.0,A*31:87,Flu_Cy_lymphodepletion,1000000.0,2024-02-20T00:00:00Z,Dosed
S00381,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,25,M,38.7,White,DEU,SITE_033,32.72,BCVA_letters,1,1.09,A*02:16,None,60000000000000.0,2023-09-01T00:00:00Z,Dosed
S00382,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,48,M,58.2,White,FRA,SITE_022,76.16,BM_plasma_pct,3,0.0,A*19:03,Flu_Cy_lymphodepletion,5000000.0,2023-03-24T00:00:00Z,Dosed
S00383,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,53,M,50.1,Hispanic or Latino,USA,SITE_018,1.66,LDH_x_ULN,2,0.0,A*07:32,Flu_Cy_lymphodepletion,1000000.0,2023-11-16T00:00:00Z,Dosed
S00384,D66,Hemophilia A,AAV,AAV-FVIII,61,F,55.2,White,ITA,SITE_027,3.24,FVIII_pct,1,12.26,A*11:67,None,110000000000000.0,2024-06-03T00:00:00Z,Screen Failure - nAb+
S00385,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,37,F,40.0,White,ESP,SITE_025,7.08,Hb_g_dL,6,0.0,A*21:50,Busulfan_reduced,5000000.0,2023-06-21T00:00:00Z,Dosed
S00386,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,1,F,8.6,White,USA,SITE_029,4.79,GMFC_MLD,2,0.0,A*21:87,Busulfan_reduced,5000000.0,2023-08-17T00:00:00Z,Dosed
S00387,C91.00,B-ALL,CAR_T,CART-CD19,8,M,25.4,Asian,CAN,SITE_021,72.52,BM_blast_pct,6,0.0,A*27:62,Flu_Cy_lymphodepletion,1000000.0,2023-08-19T00:00:00Z,Dosed
S00388,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,M,15.9,White,USA,SITE_035,4.26,GMFC_MLD,0,0.0,A*28:63,Busulfan_reduced,3000000.0,2023-10-13T00:00:00Z,Dosed
S00389,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,24.2,White,USA,SITE_002,27.26,CHOP_INTEND,2,12.5,A*15:97,None,200000000000000.0,2023-09-23T00:00:00Z,Dosed
S00390,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,72,M,70.1,White,FRA,SITE_017,33.55,BM_plasma_pct,6,0.0,A*24:45,Flu_Cy_lymphodepletion,1000000.0,2023-04-22T00:00:00Z,Dosed
S00391,C91.00,B-ALL,CAR_T,CART-CD19,13,M,17.5,White,USA,SITE_026,41.18,BM_blast_pct,5,0.0,A*01:97,Flu_Cy_lymphodepletion,2000000.0,2023-08-04T00:00:00Z,Dosed
S00392,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,12.6,Not Reported,FRA,SITE_011,25.05,NSAA,0,3.62,A*12:60,None,30000000000000.0,2024-06-16T00:00:00Z,Dosed
S00393,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,64,F,68.0,White,AUS,SITE_028,68.75,mNIS_plus_7,1,0.0,A*32:95,None,1.0,2023-12-19T00:00:00Z,Dosed
S00394,C91.00,B-ALL,CAR_T,CART-CD19,12,M,13.9,White,USA,SITE_017,60.9,BM_blast_pct,5,0.0,A*21:82,Flu_Cy_lymphodepletion,10000000.0,2023-06-01T00:00:00Z,Dosed
S00395,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,18.5,White,AUS,SITE_005,15.13,CHOP_INTEND,0,0.25,A*28:10,None,15000000000000.0,2023-01-16T00:00:00Z,Dosed
S00396,D66,Hemophilia A,AAV,AAV-FVIII,35,M,44.0,White,JPN,SITE_030,3.8,FVIII_pct,0,3.15,A*03:45,None,200000000000000.0,2023-03-03T00:00:00Z,Dosed
S00397,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,53,M,46.9,White,USA,SITE_040,3.05,LDH_x_ULN,4,0.0,A*07:31,Flu_Cy_lymphodepletion,1000000.0,2024-02-08T00:00:00Z,Dosed
S00398,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,19,M,20.5,Black or African American,GBR,SITE_036,8.23,Hb_g_dL,2,0.0,A*14:26,Treosulfan,5000000.0,2024-01-08T00:00:00Z,Dosed
S00399,D66,Hemophilia A,AAV,AAV-FVIII,51,F,42.6,White,USA,SITE_020,4.47,FVIII_pct,1,5.5,A*22:65,None,15000000000000.0,2024-02-27T00:00:00Z,Screen Failure - nAb+
S00400,D66,Hemophilia A,AAV,AAV-FVIII,52,M,52.2,Black or African American,DEU,SITE_011,4.42,FVIII_pct,0,56.62,A*01:60,None,60000000000000.0,2023-05-29T00:00:00Z,Dosed
S00401,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,15,M,28.4,Hispanic or Latino,GBR,SITE_028,6.12,Hb_g_dL,2,0.0,A*20:46,Busulfan_reduced,5000000.0,2024-05-15T00:00:00Z,Dosed
S00402,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,45,F,48.9,Asian,GBR,SITE_038,55.59,BM_plasma_pct,5,0.0,A*11:42,Flu_Cy_lymphodepletion,2000000.0,2024-03-16T00:00:00Z,Dosed
S00403,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,69,F,57.3,Hispanic or Latino,USA,SITE_009,1.13,LDH_x_ULN,4,0.0,A*14:93,Flu_Cy_lymphodepletion,10000000.0,2024-04-29T00:00:00Z,Dosed
S00404,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,M,7.9,Black or African American,GBR,SITE_032,32.42,CHOP_INTEND,0,12.93,A*31:90,None,60000000000000.0,2023-04-27T00:00:00Z,Screen Failure - nAb+
S00405,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,8,F,27.2,White,USA,SITE_003,3.54,GMFC_MLD,1,0.0,A*28:41,Busulfan_reduced,3000000.0,2023-08-29T00:00:00Z,Dosed
S00406,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,37,M,34.4,White,USA,SITE_029,79.87,BM_plasma_pct,3,0.0,A*12:72,Flu_Cy_lymphodepletion,1000000.0,2023-04-20T00:00:00Z,Dosed
S00407,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,29,M,32.6,Black or African American,USA,SITE_002,9.19,Hb_g_dL,4,0.0,A*08:26,Treosulfan,5000000.0,2023-06-01T00:00:00Z,Dosed
S00408,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,78,F,73.4,Hispanic or Latino,USA,SITE_031,3.47,LDH_x_ULN,3,0.0,A*31:54,Flu_Cy_lymphodepletion,1000000.0,2023-12-01T00:00:00Z,Dosed
S00409,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,1,M,19.1,White,USA,SITE_030,31.0,CHOP_INTEND,0,37.62,A*32:64,None,60000000000000.0,2023-06-24T00:00:00Z,Screen Failure - nAb+
S00410,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,6,F,24.0,White,USA,SITE_039,3.07,GMFC_MLD,0,0.0,A*20:80,Treosulfan,3000000.0,2023-01-10T00:00:00Z,Dosed
S00411,C91.00,B-ALL,CAR_T,CART-CD19,3,M,8.7,Other,USA,SITE_040,82.02,BM_blast_pct,5,0.0,A*25:51,Flu_Cy_lymphodepletion,2000000.0,2024-03-25T00:00:00Z,Dosed
S00412,C91.00,B-ALL,CAR_T,CART-CD19,6,M,17.1,White,FRA,SITE_036,69.95,BM_blast_pct,6,0.0,A*33:51,Flu_Cy_lymphodepletion,2000000.0,2024-01-13T00:00:00Z,Dosed
S00413,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,M,16.2,Black or African American,FRA,SITE_036,28.62,CHOP_INTEND,2,2.09,A*14:47,None,15000000000000.0,2023-11-14T00:00:00Z,Dosed
S00414,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,56,M,56.9,White,DEU,SITE_021,38.28,BM_plasma_pct,6,0.0,A*21:21,Flu_Cy_lymphodepletion,1000000.0,2023-08-18T00:00:00Z,Dosed
S00415,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,F,23.9,White,ESP,SITE_032,15.63,CHOP_INTEND,0,53.08,A*04:83,None,30000000000000.0,2024-05-09T00:00:00Z,Screen Failure - nAb+
S00416,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,17,M,40.4,Black or African American,FRA,SITE_009,9.04,Hb_g_dL,3,0.0,A*18:25,Busulfan_reduced,2000000.0,2023-07-14T00:00:00Z,Dosed
S00417,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,M,17.0,White,AUS,SITE_032,25.17,NSAA,2,5.68,A*26:59,None,200000000000000.0,2024-02-22T00:00:00Z,Dosed
S00418,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,53,F,52.2,Hispanic or Latino,FRA,SITE_031,2.11,LDH_x_ULN,2,0.0,A*22:06,Flu_Cy_lymphodepletion,5000000.0,2024-02-05T00:00:00Z,Dosed
S00419,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,18.1,White,GBR,SITE_001,21.15,NSAA,0,3.46,A*11:51,None,15000000000000.0,2023-05-10T00:00:00Z,Dosed
S00420,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,53,M,40.1,White,USA,SITE_006,31.49,BM_plasma_pct,3,0.0,A*33:31,Flu_Cy_lymphodepletion,10000000.0,2024-05-02T00:00:00Z,Dosed
S00421,C91.00,B-ALL,CAR_T,CART-CD19,16,M,40.9,Black or African American,JPN,SITE_034,40.36,BM_blast_pct,3,0.0,A*11:34,Flu_Cy_lymphodepletion,2000000.0,2023-09-04T00:00:00Z,Dosed
S00422,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,15.1,White,USA,SITE_037,19.53,CHOP_INTEND,1,3.75,A*10:55,None,15000000000000.0,2023-01-11T00:00:00Z,Dosed
S00423,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,2,F,19.7,Black or African American,GBR,SITE_022,18.36,CHOP_INTEND,2,0.95,A*06:31,None,110000000000000.0,2024-01-16T00:00:00Z,Screen Failure - nAb+
S00424,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,14.9,Other,AUS,SITE_027,13.78,CHOP_INTEND,0,4.4,A*13:65,None,60000000000000.0,2024-06-19T00:00:00Z,Dosed
S00425,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,71,F,63.3,Black or African American,USA,SITE_002,69.65,mNIS_plus_7,0,0.0,A*23:37,None,0.7,2024-04-30T00:00:00Z,Dosed
S00426,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,72,F,53.3,Black or African American,USA,SITE_035,1.72,LDH_x_ULN,5,0.0,A*14:85,Flu_Cy_lymphodepletion,5000000.0,2023-06-01T00:00:00Z,Dosed
S00427,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,26,M,39.0,White,CAN,SITE_021,9.4,Hb_g_dL,3,0.0,A*34:74,Busulfan_full,2000000.0,2023-05-27T00:00:00Z,Dosed
S00428,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,77,M,61.5,Hispanic or Latino,USA,SITE_031,1.06,LDH_x_ULN,5,0.0,A*16:76,Flu_Cy_lymphodepletion,5000000.0,2024-03-01T00:00:00Z,Dosed
S00429,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,11.6,White,FRA,SITE_016,18.04,CHOP_INTEND,2,3.5,A*27:51,None,60000000000000.0,2024-04-18T00:00:00Z,Dosed
S00430,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,41,M,42.6,White,AUS,SITE_012,3.29,LDH_x_ULN,6,0.0,A*09:72,Flu_Cy_lymphodepletion,1000000.0,2023-10-21T00:00:00Z,Dosed
S00431,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,66,F,70.5,Black or African American,DEU,SITE_002,64.07,BM_plasma_pct,5,0.0,A*29:23,Flu_Cy_lymphodepletion,10000000.0,2023-10-25T00:00:00Z,Dosed
S00432,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,64,M,58.3,White,FRA,SITE_021,1.27,LDH_x_ULN,2,0.0,A*23:42,Flu_Cy_lymphodepletion,10000000.0,2024-01-15T00:00:00Z,Dosed
S00433,C91.00,B-ALL,CAR_T,CART-CD19,27,M,30.5,Not Reported,USA,SITE_028,48.11,BM_blast_pct,4,0.0,A*18:27,Flu_Cy_lymphodepletion,5000000.0,2024-06-13T00:00:00Z,Dosed
S00434,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,61,F,58.5,White,FRA,SITE_028,1.0,LDH_x_ULN,4,0.0,A*23:34,Flu_Cy_lymphodepletion,2000000.0,2023-03-25T00:00:00Z,Dosed
S00435,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,20.3,Black or African American,JPN,SITE_026,16.07,CHOP_INTEND,2,5.08,A*30:80,None,110000000000000.0,2023-03-28T00:00:00Z,Dosed
S00436,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,26.5,Black or African American,CAN,SITE_024,18.25,NSAA,0,4.75,A*30:69,None,200000000000000.0,2023-08-24T00:00:00Z,Dosed
S00437,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,32.1,White,AUS,SITE_024,23.49,NSAA,0,10.6,A*33:84,None,15000000000000.0,2024-06-13T00:00:00Z,Dosed
S00438,D67,Hemophilia B,AAV,AAV-FIX-Padua,39,F,42.0,Hispanic or Latino,USA,SITE_026,4.53,FIX_pct,2,79.14,A*09:96,None,15000000000000.0,2023-01-19T00:00:00Z,Dosed
S00439,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,F,48.4,White,USA,SITE_037,2.19,LDH_x_ULN,3,0.0,A*16:62,Flu_Cy_lymphodepletion,2000000.0,2024-05-13T00:00:00Z,Dosed
S00440,C91.00,B-ALL,CAR_T,CART-CD19,1,F,11.7,White,CAN,SITE_035,39.16,BM_blast_pct,5,0.0,A*04:11,Flu_Cy_lymphodepletion,10000000.0,2023-03-24T00:00:00Z,Dosed
S00441,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,70,F,56.7,White,AUS,SITE_023,36.8,BM_plasma_pct,3,0.0,A*17:54,Flu_Cy_lymphodepletion,5000000.0,2023-08-30T00:00:00Z,Dosed
S00442,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,24.3,Black or African American,CAN,SITE_036,15.53,NSAA,1,22.19,A*22:86,None,200000000000000.0,2023-09-15T00:00:00Z,Screen Failure - nAb+
S00443,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,60,M,65.3,White,USA,SITE_022,2.95,LDH_x_ULN,3,0.0,A*33:06,Flu_Cy_lymphodepletion,10000000.0,2023-07-03T00:00:00Z,Dosed
S00444,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,32.9,White,USA,SITE_001,20.63,NSAA,1,11.26,A*02:56,None,60000000000000.0,2024-01-09T00:00:00Z,Dosed
S00445,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,31,M,21.9,Hispanic or Latino,CAN,SITE_023,6.5,Hb_g_dL,6,0.0,A*24:13,Busulfan_reduced,3000000.0,2024-03-03T00:00:00Z,Dosed
S00446,C91.00,B-ALL,CAR_T,CART-CD19,13,M,32.1,White,AUS,SITE_012,84.57,BM_blast_pct,5,0.0,A*14:45,Flu_Cy_lymphodepletion,1000000.0,2023-02-14T00:00:00Z,Dosed
S00447,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,4,M,24.1,White,DEU,SITE_035,1.64,GMFC_MLD,2,0.0,A*06:45,Busulfan_full,8000000.0,2023-01-19T00:00:00Z,Dosed
S00448,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,62,F,59.3,White,DEU,SITE_006,36.2,mNIS_plus_7,2,0.0,A*30:71,None,1.0,2024-05-22T00:00:00Z,Dosed
S00449,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,19.6,White,USA,SITE_017,28.21,CHOP_INTEND,2,2.1,A*25:24,None,30000000000000.0,2024-01-28T00:00:00Z,Dosed
S00450,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,70,M,70.4,White,USA,SITE_020,71.99,mNIS_plus_7,2,0.0,A*27:47,None,1.0,2024-06-13T00:00:00Z,Dosed
S00451,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,0,M,13.6,White,DEU,SITE_033,20.7,CHOP_INTEND,0,4.9,A*03:34,None,30000000000000.0,2024-03-04T00:00:00Z,Dosed
S00452,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,71,F,61.8,Black or African American,USA,SITE_008,47.24,BM_plasma_pct,4,0.0,A*21:06,Flu_Cy_lymphodepletion,5000000.0,2023-07-06T00:00:00Z,Dosed
S00453,C91.00,B-ALL,CAR_T,CART-CD19,16,M,27.7,Black or African American,USA,SITE_031,46.88,BM_blast_pct,2,0.0,A*25:79,Flu_Cy_lymphodepletion,2000000.0,2023-05-21T00:00:00Z,Dosed
S00454,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,7,M,14.6,Hispanic or Latino,USA,SITE_014,17.31,NSAA,2,338.26,A*31:75,None,15000000000000.0,2023-04-11T00:00:00Z,Dosed
S00455,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,23.9,White,USA,SITE_019,17.15,CHOP_INTEND,2,22.24,A*08:04,None,30000000000000.0,2023-08-28T00:00:00Z,Dosed
S00456,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,0,F,7.8,White,USA,SITE_022,19.1,NSAA,0,1.71,A*17:21,None,30000000000000.0,2023-09-14T00:00:00Z,Dosed
S00457,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,7,M,26.9,White,DEU,SITE_035,5.53,GMFC_MLD,1,0.0,A*29:50,Busulfan_full,5000000.0,2024-01-01T00:00:00Z,Dosed
S00458,D66,Hemophilia A,AAV,AAV-FVIII,32,F,45.3,Black or African American,USA,SITE_002,2.59,FVIII_pct,1,6.57,A*01:44,None,60000000000000.0,2023-01-04T00:00:00Z,Screen Failure - nAb+
S00459,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,54,M,39.8,White,JPN,SITE_027,1.93,LDH_x_ULN,5,0.0,A*34:91,Flu_Cy_lymphodepletion,10000000.0,2023-04-29T00:00:00Z,Dosed
S00460,C91.00,B-ALL,CAR_T,CART-CD19,18,F,21.3,Asian,ITA,SITE_015,69.5,BM_blast_pct,2,0.0,A*16:49,Flu_Cy_lymphodepletion,10000000.0,2023-01-10T00:00:00Z,Dosed
S00461,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,66,F,64.3,White,CAN,SITE_008,68.34,mNIS_plus_7,2,0.0,A*29:55,None,1.0,2023-11-03T00:00:00Z,Dosed
S00462,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,2,M,10.7,Asian,DEU,SITE_039,19.72,NSAA,2,3.22,A*16:43,None,30000000000000.0,2023-11-09T00:00:00Z,Dosed
S00463,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,4,F,16.8,Other,ESP,SITE_018,0.1,GMFC_MLD,0,0.0,A*09:71,Busulfan_reduced,8000000.0,2023-10-19T00:00:00Z,Dosed
S00464,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,17,F,29.0,Black or African American,DEU,SITE_029,7.65,Hb_g_dL,3,0.0,A*14:83,Busulfan_full,5000000.0,2023-08-12T00:00:00Z,Dosed
S00465,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,67,F,70.8,White,USA,SITE_028,89.21,mNIS_plus_7,0,0.0,A*12:67,None,1.0,2024-04-23T00:00:00Z,Dosed
S00466,C91.00,B-ALL,CAR_T,CART-CD19,13,M,16.8,Hispanic or Latino,USA,SITE_018,42.87,BM_blast_pct,4,0.0,A*24:43,Flu_Cy_lymphodepletion,2000000.0,2023-08-02T00:00:00Z,Dosed
S00467,C91.00,B-ALL,CAR_T,CART-CD19,3,M,14.5,White,JPN,SITE_032,38.11,BM_blast_pct,3,0.0,A*25:08,Flu_Cy_lymphodepletion,10000000.0,2023-06-22T00:00:00Z,Dosed
S00468,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,F,22.9,Black or African American,USA,SITE_025,1.67,GMFC_MLD,0,0.0,A*28:50,Busulfan_full,8000000.0,2023-06-03T00:00:00Z,Dosed
S00469,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,F,8.0,White,USA,SITE_016,20.2,NSAA,0,10.49,A*12:43,None,30000000000000.0,2023-05-13T00:00:00Z,Screen Failure - nAb+
S00470,D67,Hemophilia B,AAV,AAV-FIX-Padua,56,F,55.5,Black or African American,JPN,SITE_009,3.72,FIX_pct,0,403.62,A*14:59,None,110000000000000.0,2024-05-15T00:00:00Z,Dosed
S00471,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,32,M,29.5,Hispanic or Latino,ITA,SITE_034,6.78,Hb_g_dL,2,0.0,A*29:39,Busulfan_reduced,5000000.0,2023-06-24T00:00:00Z,Dosed
S00472,D66,Hemophilia A,AAV,AAV-FVIII,30,M,34.1,Black or African American,USA,SITE_009,1.88,FVIII_pct,1,6.69,A*22:88,None,15000000000000.0,2024-03-03T00:00:00Z,Dosed
S00473,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,M,21.7,Hispanic or Latino,USA,SITE_029,24.3,CHOP_INTEND,1,118.35,A*30:25,None,15000000000000.0,2023-09-03T00:00:00Z,Dosed
S00474,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,0,M,14.2,Other,USA,SITE_035,25.41,NSAA,0,24.16,A*20:91,None,110000000000000.0,2023-08-09T00:00:00Z,Dosed
S00475,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,22,M,30.3,White,USA,SITE_014,6.86,Hb_g_dL,5,0.0,A*17:32,Treosulfan,3000000.0,2023-06-04T00:00:00Z,Dosed
S00476,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,21,F,26.6,White,FRA,SITE_026,6.61,Hb_g_dL,5,0.0,A*13:86,Treosulfan,5000000.0,2023-12-08T00:00:00Z,Dosed
S00477,D66,Hemophilia A,AAV,AAV-FVIII,41,F,39.9,Black or African American,ITA,SITE_040,3.13,FVIII_pct,1,2.97,A*28:47,None,15000000000000.0,2024-03-08T00:00:00Z,Dosed
S00478,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,74,M,56.3,White,ESP,SITE_036,48.22,mNIS_plus_7,2,0.0,A*32:24,None,0.3,2024-04-08T00:00:00Z,Dosed
S00479,C91.00,B-ALL,CAR_T,CART-CD19,1,M,25.3,White,ESP,SITE_007,56.61,BM_blast_pct,4,0.0,A*09:21,Flu_Cy_lymphodepletion,1000000.0,2023-07-05T00:00:00Z,Dosed
S00480,D66,Hemophilia A,AAV,AAV-FVIII,45,M,51.5,Black or African American,USA,SITE_023,1.28,FVIII_pct,1,5.58,A*24:86,None,60000000000000.0,2023-11-11T00:00:00Z,Screen Failure - nAb+
S00481,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,19,M,16.6,Asian,GBR,SITE_037,7.64,Hb_g_dL,5,0.0,A*08:64,Busulfan_full,5000000.0,2023-03-28T00:00:00Z,Dosed
S00482,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,5,M,19.2,White,USA,SITE_037,15.44,NSAA,1,1.4,A*01:27,None,15000000000000.0,2023-09-22T00:00:00Z,Dosed
S00483,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,54,M,49.2,White,GBR,SITE_040,79.22,mNIS_plus_7,1,0.0,A*12:22,None,0.7,2023-12-24T00:00:00Z,Dosed
S00484,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,24,M,29.6,White,ESP,SITE_031,8.6,Hb_g_dL,6,0.0,A*24:80,Busulfan_reduced,2000000.0,2023-05-07T00:00:00Z,Dosed
S00485,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,9.7,White,USA,SITE_012,22.66,CHOP_INTEND,2,42.83,A*17:94,None,30000000000000.0,2023-11-18T00:00:00Z,Dosed
S00486,D66,Hemophilia A,AAV,AAV-FVIII,18,F,27.8,Black or African American,CAN,SITE_014,2.74,FVIII_pct,1,22.18,A*25:59,None,30000000000000.0,2023-01-14T00:00:00Z,Dosed
S00487,D66,Hemophilia A,AAV,AAV-FVIII,33,F,42.1,White,GBR,SITE_025,1.79,FVIII_pct,1,0.66,A*31:56,None,60000000000000.0,2024-05-28T00:00:00Z,Screen Failure - nAb+
S00488,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,30,M,42.6,White,JPN,SITE_017,10.0,Hb_g_dL,3,0.0,A*21:23,Treosulfan,5000000.0,2024-06-06T00:00:00Z,Dosed
S00489,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,75,M,73.0,Black or African American,USA,SITE_031,95.35,mNIS_plus_7,0,0.0,A*19:27,None,0.1,2023-10-24T00:00:00Z,Dosed
S00490,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,34,F,44.4,White,ESP,SITE_007,20.57,BCVA_letters,1,2.56,A*05:28,None,30000000000000.0,2024-06-13T00:00:00Z,Dosed
S00491,C91.00,B-ALL,CAR_T,CART-CD19,23,M,30.9,White,ITA,SITE_017,54.43,BM_blast_pct,3,0.0,A*33:50,Flu_Cy_lymphodepletion,5000000.0,2024-06-15T00:00:00Z,Dosed
S00492,C91.00,B-ALL,CAR_T,CART-CD19,20,M,29.6,White,CAN,SITE_029,36.34,BM_blast_pct,4,0.0,A*20:43,Flu_Cy_lymphodepletion,2000000.0,2023-07-14T00:00:00Z,Dosed
S00493,C91.00,B-ALL,CAR_T,CART-CD19,8,M,21.6,White,USA,SITE_030,43.88,BM_blast_pct,6,0.0,A*28:41,Flu_Cy_lymphodepletion,1000000.0,2024-02-14T00:00:00Z,Dosed
S00494,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,4.0,Black or African American,USA,SITE_028,8.57,Hb_g_dL,5,0.0,A*29:96,Treosulfan,2000000.0,2023-11-01T00:00:00Z,Dosed
S00495,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,69,M,49.6,Asian,USA,SITE_019,1.49,LDH_x_ULN,6,0.0,A*10:57,Flu_Cy_lymphodepletion,5000000.0,2024-01-06T00:00:00Z,Dosed
S00496,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,44,F,45.3,Other,AUS,SITE_004,42.42,BCVA_letters,0,33.4,A*28:76,None,60000000000000.0,2023-01-30T00:00:00Z,Dosed
S00497,D66,Hemophilia A,AAV,AAV-FVIII,35,F,37.4,White,USA,SITE_023,3.21,FVIII_pct,1,0.8,A*02:13,None,200000000000000.0,2024-02-26T00:00:00Z,Screen Failure - nAb+
S00498,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,57,M,61.1,White,CAN,SITE_014,99.96,mNIS_plus_7,1,0.0,A*34:50,None,0.7,2023-01-30T00:00:00Z,Dosed
S00499,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,18,M,23.5,Black or African American,USA,SITE_023,5.28,Hb_g_dL,5,0.0,A*32:26,Busulfan_full,2000000.0,2024-03-26T00:00:00Z,Dosed
S00500,D67,Hemophilia B,AAV,AAV-FIX-Padua,29,M,34.3,White,USA,SITE_027,1.35,FIX_pct,2,23.31,A*17:10,None,110000000000000.0,2023-07-11T00:00:00Z,Dosed
S00501,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,74,F,72.5,White,USA,SITE_040,3.82,LDH_x_ULN,6,0.0,A*18:13,Flu_Cy_lymphodepletion,10000000.0,2023-08-13T00:00:00Z,Dosed
S00502,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,66,F,44.2,Asian,USA,SITE_005,46.59,BM_plasma_pct,5,0.0,A*25:83,Flu_Cy_lymphodepletion,5000000.0,2024-01-18T00:00:00Z,Dosed
S00503,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,67,M,70.7,White,AUS,SITE_025,55.21,BM_plasma_pct,2,0.0,A*34:52,Flu_Cy_lymphodepletion,2000000.0,2023-12-22T00:00:00Z,Dosed
S00504,D67,Hemophilia B,AAV,AAV-FIX-Padua,35,M,31.1,White,USA,SITE_035,1.09,FIX_pct,2,12.2,A*19:31,None,30000000000000.0,2024-02-07T00:00:00Z,Screen Failure - nAb+
S00505,D67,Hemophilia B,AAV,AAV-FIX-Padua,26,M,29.4,Hispanic or Latino,ITA,SITE_005,2.77,FIX_pct,2,41.86,A*26:74,None,200000000000000.0,2023-10-21T00:00:00Z,Dosed
S00506,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,62,M,52.9,White,DEU,SITE_007,1.06,LDH_x_ULN,6,0.0,A*02:33,Flu_Cy_lymphodepletion,10000000.0,2023-03-25T00:00:00Z,Dosed
S00507,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,13,M,12.6,Other,USA,SITE_031,7.62,Hb_g_dL,6,0.0,A*20:44,Busulfan_full,3000000.0,2023-11-25T00:00:00Z,Dosed
S00508,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,58,M,74.1,Black or African American,USA,SITE_035,1.31,LDH_x_ULN,2,0.0,A*15:48,Flu_Cy_lymphodepletion,10000000.0,2023-08-27T00:00:00Z,Dosed
S00509,D67,Hemophilia B,AAV,AAV-FIX-Padua,33,M,31.6,White,CAN,SITE_033,4.66,FIX_pct,0,5.68,A*14:75,None,15000000000000.0,2023-11-17T00:00:00Z,Dosed
S00510,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,23.2,Black or African American,ITA,SITE_011,17.33,CHOP_INTEND,0,18.46,A*31:26,None,60000000000000.0,2023-09-06T00:00:00Z,Dosed
S00511,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,13.0,White,ESP,SITE_033,21.98,CHOP_INTEND,1,8.28,A*03:04,None,60000000000000.0,2023-08-29T00:00:00Z,Screen Failure - nAb+
S00512,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,62,F,54.1,White,JPN,SITE_021,2.95,LDH_x_ULN,2,0.0,A*12:58,Flu_Cy_lymphodepletion,2000000.0,2023-03-25T00:00:00Z,Dosed
S00513,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,M,13.2,White,AUS,SITE_035,32.92,CHOP_INTEND,0,2.55,A*17:65,None,60000000000000.0,2023-11-18T00:00:00Z,Dosed
S00514,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,36,M,40.6,Black or African American,AUS,SITE_038,6.71,Hb_g_dL,5,0.0,A*20:72,Treosulfan,5000000.0,2023-06-26T00:00:00Z,Dosed
S00515,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,12,M,11.6,White,GBR,SITE_008,8.22,Hb_g_dL,5,0.0,A*30:31,Busulfan_reduced,3000000.0,2024-02-04T00:00:00Z,Dosed
S00516,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,6,F,25.0,Asian,GBR,SITE_040,27.88,NSAA,1,132.11,A*11:26,None,60000000000000.0,2023-02-19T00:00:00Z,Dosed
S00517,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,34,F,33.5,White,USA,SITE_001,8.53,Hb_g_dL,2,0.0,A*34:58,Busulfan_full,5000000.0,2023-04-10T00:00:00Z,Dosed
S00518,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,64,M,59.8,Black or African American,ESP,SITE_014,2.19,LDH_x_ULN,4,0.0,A*02:08,Flu_Cy_lymphodepletion,10000000.0,2023-01-20T00:00:00Z,Dosed
S00519,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,M,19.8,Hispanic or Latino,DEU,SITE_015,13.63,CHOP_INTEND,0,10.52,A*32:60,None,200000000000000.0,2024-05-12T00:00:00Z,Dosed
S00520,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,47,M,46.0,Asian,GBR,SITE_010,1.48,LDH_x_ULN,4,0.0,A*13:28,Flu_Cy_lymphodepletion,10000000.0,2023-06-29T00:00:00Z,Dosed
S00521,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,55,F,57.8,White,ESP,SITE_028,73.44,BM_plasma_pct,2,0.0,A*25:58,Flu_Cy_lymphodepletion,10000000.0,2023-06-10T00:00:00Z,Dosed
S00522,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,30,F,46.8,Black or African American,JPN,SITE_009,7.65,Hb_g_dL,4,0.0,A*26:52,Busulfan_reduced,3000000.0,2023-12-18T00:00:00Z,Dosed
S00523,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,F,4.4,White,ESP,SITE_015,25.47,NSAA,1,2.15,A*22:84,None,110000000000000.0,2024-03-05T00:00:00Z,Screen Failure - nAb+
S00524,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,62,F,52.8,Asian,AUS,SITE_002,55.26,mNIS_plus_7,2,0.0,A*21:15,None,0.3,2024-06-22T00:00:00Z,Dosed
S00525,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,3,F,19.7,Black or African American,GBR,SITE_011,28.04,CHOP_INTEND,0,58.54,A*08:20,None,200000000000000.0,2024-03-12T00:00:00Z,Dosed
S00526,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,26,M,21.3,Asian,ESP,SITE_027,4.76,Hb_g_dL,2,0.0,A*14:45,Busulfan_full,5000000.0,2023-04-25T00:00:00Z,Dosed
S00527,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,3,F,4.0,White,ITA,SITE_025,1.87,GMFC_MLD,1,0.0,A*11:32,Busulfan_reduced,8000000.0,2023-02-21T00:00:00Z,Dosed
S00528,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,M,17.4,White,USA,SITE_005,4.38,GMFC_MLD,1,0.0,A*18:35,Busulfan_full,3000000.0,2024-02-13T00:00:00Z,Dosed
S00529,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,72,M,68.4,White,USA,SITE_024,3.18,LDH_x_ULN,2,0.0,A*11:46,Flu_Cy_lymphodepletion,2000000.0,2023-01-17T00:00:00Z,Dosed
S00530,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,13,M,43.5,White,CAN,SITE_020,9.14,Hb_g_dL,2,0.0,A*01:91,Treosulfan,2000000.0,2023-12-15T00:00:00Z,Dosed
S00531,C91.00,B-ALL,CAR_T,CART-CD19,5,F,26.4,Black or African American,USA,SITE_015,53.79,BM_blast_pct,6,0.0,A*23:32,Flu_Cy_lymphodepletion,2000000.0,2023-07-18T00:00:00Z,Dosed
S00532,C91.00,B-ALL,CAR_T,CART-CD19,17,F,18.6,Other,JPN,SITE_031,33.4,BM_blast_pct,2,0.0,A*13:80,Flu_Cy_lymphodepletion,1000000.0,2024-03-18T00:00:00Z,Dosed
S00533,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,33,F,40.1,Asian,DEU,SITE_015,6.15,Hb_g_dL,5,0.0,A*16:07,Busulfan_full,2000000.0,2023-11-07T00:00:00Z,Dosed
S00534,C91.00,B-ALL,CAR_T,CART-CD19,28,M,38.8,White,USA,SITE_008,66.99,BM_blast_pct,4,0.0,A*07:14,Flu_Cy_lymphodepletion,1000000.0,2023-12-13T00:00:00Z,Dosed
S00535,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,1,M,22.8,White,ESP,SITE_013,29.9,CHOP_INTEND,2,9.78,A*32:51,None,15000000000000.0,2023-02-22T00:00:00Z,Dosed
S00536,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,7.6,White,CAN,SITE_028,15.8,NSAA,2,11.19,A*08:52,None,30000000000000.0,2023-12-22T00:00:00Z,Dosed
S00537,D67,Hemophilia B,AAV,AAV-FIX-Padua,32,M,44.3,White,CAN,SITE_002,4.65,FIX_pct,2,6.13,A*28:15,None,15000000000000.0,2023-08-11T00:00:00Z,Screen Failure - nAb+
S00538,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,7,M,22.2,White,AUS,SITE_013,26.05,NSAA,1,89.54,A*09:31,None,200000000000000.0,2023-05-03T00:00:00Z,Dosed
S00539,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,3,M,17.7,White,USA,SITE_019,26.25,NSAA,1,51.59,A*02:17,None,30000000000000.0,2023-08-05T00:00:00Z,Screen Failure - nAb+
S00540,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,73,F,60.8,White,USA,SITE_019,1.98,LDH_x_ULN,3,0.0,A*04:21,Flu_Cy_lymphodepletion,10000000.0,2023-12-02T00:00:00Z,Dosed
S00541,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,M,29.2,White,USA,SITE_012,2.58,GMFC_MLD,0,0.0,A*16:67,Busulfan_full,3000000.0,2024-04-05T00:00:00Z,Dosed
S00542,H35.50,Leber Congenital Amaurosis,AAV,AAV-RPE65,37,M,45.6,Asian,CAN,SITE_030,39.45,BCVA_letters,1,4.77,A*29:34,None,30000000000000.0,2024-03-29T00:00:00Z,Dosed
S00543,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,62,M,67.6,White,JPN,SITE_001,3.89,LDH_x_ULN,5,0.0,A*19:02,Flu_Cy_lymphodepletion,5000000.0,2023-08-23T00:00:00Z,Dosed
S00544,E75.25,Metachromatic Leukodystrophy,LENTIVIRAL,LV-ARSA,2,M,27.3,Black or African American,ITA,SITE_031,2.73,GMFC_MLD,2,0.0,A*31:29,Treosulfan,3000000.0,2023-06-28T00:00:00Z,Dosed
S00545,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,1,F,15.4,White,GBR,SITE_023,23.39,NSAA,0,8.49,A*09:92,None,200000000000000.0,2023-07-16T00:00:00Z,Dosed
S00546,D66,Hemophilia A,AAV,AAV-FVIII,18,M,18.9,White,ITA,SITE_027,1.62,FVIII_pct,2,6.64,A*07:07,None,110000000000000.0,2024-03-15T00:00:00Z,Dosed
S00547,D56.1,Beta-Thalassemia (TDT),CRISPR,CRISPR-HbF,21,F,35.5,White,USA,SITE_005,6.71,Hb_g_dL,6,0.0,A*08:84,Treosulfan,5000000.0,2023-09-10T00:00:00Z,Dosed
S00548,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,4,M,10.8,Black or African American,ESP,SITE_018,24.22,CHOP_INTEND,2,16.41,A*20:48,None,60000000000000.0,2023-11-28T00:00:00Z,Dosed
S00549,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,69,F,67.8,White,CAN,SITE_023,2.9,LDH_x_ULN,5,0.0,A*32:04,Flu_Cy_lymphodepletion,2000000.0,2023-04-08T00:00:00Z,Dosed
S00550,D66,Hemophilia A,AAV,AAV-FVIII,52,M,58.8,Hispanic or Latino,ITA,SITE_019,3.19,FVIII_pct,2,4.3,A*03:06,None,30000000000000.0,2023-11-19T00:00:00Z,Dosed
S00551,D66,Hemophilia A,AAV,AAV-FVIII,24,F,38.9,Black or African American,JPN,SITE_012,3.61,FVIII_pct,1,53.72,A*22:15,None,30000000000000.0,2023-02-15T00:00:00Z,Dosed
S00552,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,7,M,12.0,White,AUS,SITE_022,22.6,NSAA,1,5.53,A*30:60,None,200000000000000.0,2024-02-01T00:00:00Z,Screen Failure - nAb+
S00553,G71.01,Duchenne Muscular Dystrophy,AAV,AAV-microdys,4,M,22.5,White,ESP,SITE_008,19.89,NSAA,0,1.6,A*03:42,None,15000000000000.0,2023-10-05T00:00:00Z,Screen Failure - nAb+
S00554,C90.00,Multiple Myeloma,CAR_T,CART-BCMA,50,M,40.2,White,USA,SITE_005,69.2,BM_plasma_pct,5,0.0,A*02:37,Flu_Cy_lymphodepletion,2000000.0,2023-12-03T00:00:00Z,Dosed
S00555,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,6,F,14.2,White,GBR,SITE_008,32.08,CHOP_INTEND,0,23.03,A*16:19,None,200000000000000.0,2023-07-18T00:00:00Z,Dosed
S00556,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,27,F,40.7,White,GBR,SITE_032,7.67,Hb_g_dL,5,0.0,A*18:02,Busulfan_full,3000000.0,2023-03-09T00:00:00Z,Dosed
S00557,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,15,F,25.2,Hispanic or Latino,USA,SITE_015,9.33,Hb_g_dL,5,0.0,A*33:61,Busulfan_reduced,5000000.0,2024-01-05T00:00:00Z,Dosed
S00558,D67,Hemophilia B,AAV,AAV-FIX-Padua,20,M,32.0,White,GBR,SITE_040,4.02,FIX_pct,1,76.58,A*29:86,None,30000000000000.0,2023-07-21T00:00:00Z,Dosed
S00559,E85.4,ATTR Amyloidosis,LNP_mRNA,LNP-TTR-edit,66,F,66.9,White,JPN,SITE_003,45.62,mNIS_plus_7,2,0.0,A*27:11,None,1.0,2023-05-17T00:00:00Z,Dosed
S00560,D67,Hemophilia B,AAV,AAV-FIX-Padua,40,M,32.3,Asian,ITA,SITE_001,1.5,FIX_pct,0,13.82,A*23:84,None,30000000000000.0,2023-01-30T00:00:00Z,Dosed
S00561,G12.0,SMA Type 1,AAV,AAV-SMN1-rep,5,M,8.8,Asian,ESP,SITE_022,20.36,CHOP_INTEND,2,0.83,A*31:77,None,110000000000000.0,2023-12-01T00:00:00Z,Dosed
S00562,D57.1,Sickle Cell Disease,CRISPR,CRISPR-BCL11A,21,F,25.9,Black or African American,ITA,SITE_026,6.79,Hb_g_dL,2,0.0,A*18:81,Busulfan_full,5000000.0,2023-03-11T00:00:00Z,Dosed
S00563,C83.30,Large B-Cell Lymphoma,CAR_T,CART-CD19-41BB,55,F,49.0,White,USA,SITE_027,3.4,LDH_x_ULN,6,0.0,A*27:87,Flu_Cy_lymphodepletion,10000000.0,2023-12-18T00:00:00Z,Dosed
S00564,C91.00,B-ALL,CAR_T,CART-CD19,19,F,32.0,White,ITA,SITE_036,69.25,BM_blast_pct,5,0.0,A*31:74,Flu_Cy_lymphodepletion,1000000.0,2023-09-22T00:00:00Z,Dosed